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A Sample of Attendees from the Last Two Years… TITLE COMPANY VP A sample of attendees from the last two years… TITLE COMPANY VP Value & Access Ipsen Biopharmaceuticals Inc VP US Commercial Raptor Pharmaceuticals VP Specialty Sales ASD Healthcare VP Software Engineering Digital Infuzion Inc VP Scientific Affairs Fibrocell Science Inc VP Scientific & Regulatory Strategy & Ops Cato Research VP Scientific & Regulatory Strategy & Ops Cato Research VP Scientific & Regulatory Affairs PhRMA VP Sales BDI Pharma Inc VP Regulatory Affairs Cote Orphan LLC VP Regulatory Affairs Horizon Pharma VP Regulatory Affairs Amicus Therapeutics Inc VP Regulatory Affairs ImmunoGen Inc VP Regulatory & Quality Stealth BioTherapeutics VP Regulatory & Quality Stealth BioTherapeutics VP Public Policy NORD VP Public Policy Immune Deficiency Foundation VP Programs & Education CurePSP Foundation for PSP VP President Patient Svcs National Organization for Rare Disorders VP Pharma Technology & Innovation Codexis VP Payer Insights and Access Pfizer Inc VP Patient Relations & Medical Affairs Pulmonary Fibrosis Foundation VP Patient Engagement Aegerion Pharmaceuticals VP Patient Engagement Aegerion Pharmaceuticals VP Patient Advocacy Catalyst Pharmaceuticals VP Patient & Market Acess Aegerion Pharmaceuticals VP Ops & Patient Access Sobi Inc VP Ops & Corp Partnerships The Sturge Weber Foundation VP Ops Agilis Biotherapeutics LLC VP Ops Agilis Biotherapeutics LLC VP Mktg & Bus Dev Digital Infuzion Inc VP Mktg & Bus Dev Digital Infuzion Inc VP Medical Affairs Jazz Pharmaceuticals VP Medical Intellia Therapeutics VP Marketing Orphan Bus Unit Horizon Pharma VP Manufacturer Relations BDI Pharma VP Managed Markets Zogenix VP Information Technology National Organization for Rare Disorders VP Information Technology National Organization for Rare Disorders VP Industry Relations Cardinal Health VP Health Outcomes Walgreens VP Health Outcomes Walgreen Co VP Health IT Strategy & Biomedical Consulting Digital Infuzion Inc VP Group Editor Neurology Reviews Frontline Medical Communications Inc VP Group Editor Neurology Reviews Frontline Medical Communications Inc VP Govt Relations Genzyme a Sanofi Company VP Govt Affairs & Public Policy Vertex VP Govt Affairs & Public Policy Vertex VP Govt Affairs & Advocacy BioMarin VP Govt Affairs & Advocacy BioMarin VP Global Mktg, Ops & Training Aegerion Pharmaceuticals VP Global Health Policy & Govt Affairs Sarepta Therapeutics VP Global Health Policy & Govt Affairs Sarepta Therapeutics VP Global Clinical Science Horizon Pharma VP Genetic Services Patient Crossroads VP Genetic Services Patient Crossroads VP Epidemiology Evidera VP Endo Onco Sales & Marketing Ipsen Biopharmaceuticals Inc VP Educational Initiatives National Organization for Rare Disorders VP Educational Initiatives National Organization for Rare Disorders VP Development American Multiple Endocrine Neoplasia Support VP Dev & Mktg Variant Pharmaceuticals VP Dev AMEN Support VP Corporate Dev Variant Pharmaceuticals VP Corp Dev REGENXBIO Inc VP Corp Affairs Jazz Pharmaceuticals VP Compliance Dohmen Life Science Services VP Communications Ipsen Biopharmaceuticals Inc VP Commercial Strategy & Advocacy Aegerion Pharmaceuticals VP Commercial Ops Recordati Rare Diseases Inc VP Commercial Operations Corcept Therapeutics VP Commercial Dev Rare Disease Pfizer VP Commercial & Portfolio Planning REGENXBIO Inc VP Comm Svcs Ops UBC VP Clinical Dev Dyax Corp VP Chemistry, Medicinal Chemistry Nektar Therapeutics VP Bus Ops AveXis Inc VP Bus Dev Dohmen Life Science Services VP Bus Dev FFF Enterprises VP Bus Dev Omnicare Specialty Care Group VP Bus Dev UBC / Accredo VP Bus Dev Cote Orphan LLC VP Bus Dev Express Scripts VP Bus Dev Patagonia Pharmaceuticals LLC VP Bus Dev Retrophin VP Advocacy & Outreach Cluster Headache Support Group Inc VP Access Solutions Omnicare Specialty Care Group VP Access Solutions Omnicare Specialty Care Group VP & Partner Pennside Partners Ltd VP & GM Cystic Fibrosis Svcs a Walgreens Alliance VP & Chief Commercial Officer XOMA Corporation VP A Cure In Sight VP Big Duck VP Cardinal Health Specialty Solutions VP RASopathies Network USA VP Rare Disease Report VP Avalere Health VP Caring Voice Coalition Inc VP Lynch Syndrome International VP Rare Disease Report VP Xcenda Vice Chair Board Directors Alpha 1 Foundation V PPRN Patient Partner Vasculitis Foundation US Marketing Aegerion Pharmaceuticals US Liaison Chinese Organization for Rare Disorders CORD Treasurer Alveolar Capillary Dysplasia Assoc TA Head AbbVie SVP Specialty Pharmacy Aureus Health Services SVP Regulatory & Compliance Cytokinetics SVP Regulatory & Compliance Cytokinetics SVP Rare Disease Dohmen Life Science Services SVP Legislation & Public Policy Parent Project Muscular Dystrophy SVP Global Head Site & Patient Networks Quintiles SVP Global Commercial Officer Pfizer SVP Dev & Medical CMO Swedish Orphan Biovitrum AB SVP Community Engagement Parent Project Muscular Dystrophy SVP Community Engagement Parent Project Muscular Dystrophy SVP Communications & Administration Parent Project Muscular Dystrophy SVP Immune Deficiency Foundation SVP JPA Health Communications SVP Spectrum PRF Student University of Connecticut Strategic Planning Committee Neurofibromatosis Network Strategic Advisor eMgine HealthLogics Staff Scientist Selecta Biosciences Sr Writer Pink Sheet Sr VP Technology Assessment and QA Nektar Therapeutics Sr VP Science Policy BIO Sr VP Regulatory Dyax Sr VP Public Affairs CSL Behring Sr VP Public Affairs CSL Behring Sr VP Medical & Scientific Affairs National Organization for Rare Disorders Sr VP Legislation & Public Policy Parent Project Muscular Dystrophy Sr VP Global Head Rare Diseases Genzyme Sr VP Global Bus Ops & External Affairs Horizon Pharma Sr VP Commerical Operations Lash Group Sr VP Commercial Sales Aureus Health Services Sr VP Scheer & Company Inc Sr Scientific Liaison DIA Americas Sr Research Leader Outcomes Research Evidera Sr Research Analyst Public Policy & Govt Aff Biogen Sr Regulatory Health Project Mgr Food And Drug Administration Sr Regulatory Health Project Mgr FDA Sr Regulatory Health Project Mgr FDA Sr Regulatory Group Dir Genentech Sr Regulatory Group Dir Genentech Sr Project Specialist HVMC Cincinnati Childrens Hospital Medical Ctr Sr Project Specialist HVMC Cincinnati Childrens Hospital Medical Ctr Sr Project Mgr/Drug Dev Team Lead NIH NCATS Sr Project Mgr/Drug Dev Team Lead NIH NCATS Sr Program & Policy Analyst National Institutes of Health Sr Program & Policy Analyst National Institutes of Health Sr Partner Deerfield Mgmt Sr Mgr Research & Programs CureSearch Children's Cancer Sr Mgr Operations Lash Group Sr Mgr New Rare Disease Treatments Genzyme Sr Mgr Govt Affairs & Market Access Genzyme Sr Mgr Community Relations Sarepta Therapeutics Inc Sr Mgr Commercial & Forecasting Grunenthal USA Sr Mgr ASrid Sr Mgr Biogen Sr Medical Policy Analyst FDA Ofc of Good Clinical Practice Sr Medical Officer FDA Sr Med Dir Rare Diseases Genentech Sr Marketing Mgr Baxalta Sr Health Scientist Administrator ORDR NCATS National Institutes of Health Sr Financial Case Mgr ViroPharma Charitable Foundation Sr Field Reimbursement Mgr Valeant Pharmaceuticals Sr Event Mgr EURORDIS Sr Editor Pharmaceutical Executive Sr Editor Pharmaceutical Executive Sr Dir, Alliance, Advocacy & Policy Relations Jazz Pharmaceuticals Sr Dir, Alliance, Advocacy & Policy Relations Jazz Pharmaceuticals Sr Dir Technology Dev North Carolina Biotech Center Sr Dir Research & Health Aplastic Anemia & MDS Intl Foundation Sr Dir Regulatory Policy & Intelligence Shire Sr Dir Regulatory Policy Everylife Foundation for Rare Diseases Sr Dir Regulatory Affairs Horizon Pharma Sr Dir Regulatory Affairs Shire Sr Dir Regulatory Affairs Horizon Pharma Sr Dir Regulatory Affairs Shire Sr Dir Regulatory & Quality GlycoMimetics Sr Dir Regulatory & Quality GlycoMimetics Sr Dir Regulatory & Clinical Outcomes Stealth BioTherapeutics Sr Dir Rare Disorder Walgreens Co Sr Dir Programs & Research Foundation Ichthyosis & Related Skin Types Sr Dir Pipeline Marketing Genentech Sr Dir Patient Engagement & Communications EveryLife Foundation for Rare Disease Sr Dir Patient & Physician Services UBC an Express Scripts Co Sr Dir New Product Strategy & Dev Blueprint Medicines Sr Dir New Opportunities Nektar Therapeutics Sr Dir Natl Alliance Dev Pfizer Sr Dir Multichannel Marketing Solutions Frontline Medical Communications Inc Sr Dir Mkt Access Aegerion Pharmaceuticals Sr Dir Mkt Access Aegerion Pharmaceuticals Sr Dir Medical Scientific Liaisons Aegerion Pharmaceuticals Sr Dir Med Affairs Cytokinetics Sr Dir Health Outcomes Walgreens Sr Dir Govt Affairs & Public Policy Vertex Sr Dir Govt Affairs & Public Policy Vertex Sr Dir Govt & Public Affairs Horizon Pharma Sr Dir Govt & Public Affairs Horizon Pharma Sr Dir Extenal Study Mgmt Celerion Sr Dir ERDI Pfizer Sr Dir Div Marketing AmerisourceBergen Sr Dir Communications PhRMA Sr Dir Commercial Analytics Zogenix Sr Dir Bus Dev Premier Research Sr Dir Advocacy & Awareness Pulmonary Hypertension Association Sr Dir Advocacy & Awareness Pulmonary Hypertension Association Sr Dir BioMarin Sr Dir Blueprint Medicines Sr Dir Sanofi Genzyme BioVentures Sr Dir Takeda Oncology Sr Dir Vital Therapies Inc Sr Dir Xcenda a Part of AmerisourceBergen Sr Dir AbbVie Sr Dir Prosensa Sr Dir Vital Therapies Inc Sr Clinical Study Mgr Takeda Dev Ctr Americas Inc Sr Bus Dev Dir Quintiles Sr Bus Dev Dir Quintiles Sr Bus Analyst Therapure Biopharma Inc Sr Assoc Mark Krueger & Associates Sr Assoc HealthCare Royalty Partners Sr Analyst US Government Accountability Office Sr Advisor to the Dir US
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