ISSN 00062979, Biochemistry (Moscow), 2016, Vol. 81, No. 13, pp. 16021649. © Pleiades Publishing, Ltd., 2016. Original Russian Text © N. G. Dolinnaya, A. M. Ogloblina, M. G. Yakubovskaya, 2016, published in Uspekhi Biologicheskoi Khimii, 2016, Vol. 56, pp. 53154.

REVIEW

Structure, Properties, and Biological Relevance of the DNA and RNA GQuadruplexes: Overview 50 Years after Their Discovery

N. G. Dolinnaya1*, A. M. Ogloblina2, and M. G. Yakubovskaya2

1Lomonosov Moscow State University, Department of Chemistry, 119991 Moscow, Russia; Email: [email protected] 2Blokhin Cancer Research Center, Institute of Carcinogenesis, Russian Academy of Medical Sciences, 115478 Moscow, Russia Received June 15, 2016

Abstract—Gquadruplexes (G4s), which are known to have important roles in regulation of key biological processes in both normal and pathological cells, are the most actively studied noncanonical structures of nucleic acids. In this review, we summarize the results of studies published in recent years that change significantly scientific views on various aspects of our understanding of quadruplexes. Modern notions on the polymorphism of DNA quadruplexes, on factors affecting thermo dynamics and kinetics of G4 folding–unfolding, on structural organization of multiquadruplex systems, and on conforma tional features of RNA G4s and hybrid DNA–RNA G4s are discussed. Here we report the data on location of G4 sequence motifs in the genomes of eukaryotes, bacteria, and viruses, characterize G4specific smallmolecule ligands and proteins, as well as the mechanisms of their interactions with quadruplexes. New information on the structure and stability of G4s in telomeric DNA and oncogene promoters is discussed as well as proof being provided on the occurrence of Gquadruplexes in cells. Prominence is given to novel experimental techniques (single molecule manipulations, optical and magnetic tweez ers, original chemical approaches, G4 detection in situ, incell NMR spectroscopy) that facilitate breakthroughs in the investigation of the structure and functions of Gquadruplexes.

DOI: 10.1134/S0006297916130034

Keywords: Gquadruplex thermodynamics and kinetics, multiquadruplexes, Gquadruplexspecific ligands and proteins, RNA Gquadruplexes, hybrid DNA–RNA Gquadruplexes, telomeric Gquadruplexes, Gquadruplexes in oncogene pro moters

The noncanonical DNA structures formed by con lite sequences, as well as in regulatory regions of formational rearrangement of the doublestranded genomes, specifically in oncogene promoters. Data have genome regions with specific base sequences are current been obtained by novel experimental approaches indi ly considered as a novel set of regulatory elements. Four cating that G4 play an important role in regulation of stranded Grich helical structures called the Gquadru key cellular processes [3, 4], such as replication [5, 6], plexes (G4s) are among the most amazing and actively chromosome end protection [7], transcription [8], investigated noncanonical forms of DNA. Gquadru mutagenesis [9], genome damage repair [10], DNA plexes discovered more than half a century ago as a curi recombination [11], and epigenetic processes [12, 13], ous phenomenon of guanosine gel formation now are as well as posttranscriptional events: translation [14], perceived in the scientific mind as an important structur RNA splicing, alternative polyadenylation of mRNA al element of the genome. Currently, G4 formed by RNA [15], and others. molecules have become the subject of intensive studies [1, Many reviews and even books have been dedicated to 2]. the different aspects of G4 formation, their topology, fac Nucleic acid sequences forming G4 (G4motifs) tors affecting stability and polymorphism of these struc have been found in Grich repeats of eukaryotic tures, and interaction of G4s with smallmolecule ligands genomes such as telomeric DNA, micro and minisatel [3, 1618]. However, the number of publications examin ing these noncanonical forms of nucleic acids has grown * To whom correspondence should be addressed. steadily in the last decade, which has been related mainly

1602 GQUADRUPLEXES OF NUCLEIC ACIDS 1603 with progress in investigation of their biological func in investigation of Gquadruplexes and their visualization tions. Interest in G4s is also because their formation is in biological objects. associated with widespread human diseases (cancer, car diovascular diseases, diabetes, neurodegenerative disor ders) [19, 20]. In recent years, G4s have been actively STRUCTURAL FEATURES OF NUCLEIC ACID used as components of nanostructures and lowcost GQUADRUPLEXES AND FACTORS switches that offer promise for applications in nanotech AFFECTING THEIR STABILITY nology and biology [2123]. AND CONFORMATIONAL DIVERSITY Unlike in previous review articles that considered specific issues related to G4s, in this review we summarize G4s are formed via intra or intermolecular inter all aspects of the quadruplex studies. Data from recent actions of DNA or RNA molecules containing tracts of papers that significantly change our notions on the struc oligoG (Gtracts). The central part of a quadruplex tural polymorphism, thermodynamics and kinetics of G4 (core) consists of Gtetrads, in which four guanine folding–unfolding, as well as factors affecting the equilib residues from different strands or different Gtracts (in rium between DNA duplexes and noncanonical four the case of intramolecular G4) are linked through a sys stranded , and the structural arrangement of multi tem of Hoogsteen hydrogen bonds (more precisely H quadruplexes are analyzed. In addition to these aspects, bonds formed with participation of Watson–Crick and new information on the structure and stability of G4s in Hoogsteen faces of guanine bases). Stacking interac telomeric DNA and oncogene promoters, and on confor tions of planar Gtetrads as well as additional interac mational features of RNA G4 and of hybrid DNA–RNA tions of sugarphosphate backbone fragments [24] form quadruplexes is reviewed. Also we summarized data on the specific G4 structure (Fig. 1). It should be men various classes of ligands recognizing Gquadruplexes, on tioned that the quadruplexlike structures are formed G4specific proteins and antibodies, and on the existence even during selfassociation of guanosine monophos of G4s in vivo. In this review, we present the current state phates. This is related with the specific properties of of nucleic acid Gquadruplex science including a short guanine residues, which have several mutually corre history of the development of our notions on their struc sponding electron donor and electron acceptor centers ture and properties. Special attention was paid to novel and exhibit enhanced capability for stacking interac experimental approaches that provided the breakthrough tions.

a

Antiparallel Antiparallel Mixed (“3+1”) Parallel (“chair”) (“basket”)

b c

Propeller Lateral loop Diagonal loop (doublechair reversal) loop

Fig. 1. Schematic representation of intramolecular Gquadruplexes differing in strand orientation in the quadruplex core; guanosines in syn conformation are presented in yellow, and in anticonformation – in green (a). Parallelstranded G4 with presented structure of Gtetrads and potassiumbinding sites (black circles) (b). Types of loops that connect Gtracts (c).

BIOCHEMISTRY (Moscow) Vol. 81 No. 13 2016 1604 DOLINNAYA et al.

In in vitro studies, Gquadruplexes were formed by around the Gquadruplex helix that neutralize the intermolecular interactions of two, three, or four oligonu charges of phosphate groups in the sugarphosphate cleotide molecules containing Gtracts, as well as by backbone contribute only slightly to G4 formation [28]. intramolecular folding of one oligonucleotide molecule Unlike other types of structured nucleic acids, G4 specif (Fig. 1a). A base sequence capable of intramolecular fold ically bind (coordinate) ions of mono and bivalent met 1 2 3 ing into a G4 is usually denoted as G25L G25L G25L G25, als within the highly electronegative central channel where G25 are Gtracts containing from two to five con along the axis of the G4 stem [29]; the cations lose their secutive guanosine residues, and Ln are oligonucleotide hydration shell in the process. That is why the ionic radius linkers connecting these tracts. Until recently, the quadru is a significant factor ensuring the ability of ions to stabi plex core was considered as several righthanded G lize quadruplexes. Information on location of cations tetrads [16]. Only in 2015, a lefthanded Gquadruplex inside the Gquadruplex structure and on the dynamics of analog of ZDNA was discovered using Xray analysis and their binding to DNA was obtained with the NMR spec NMR spectroscopy, which was formed during intramole troscopy and Xray study. The mechanism of a cation cular folding of the d(T(GGT)4TG(TGG)3TGTT) migration into the G4 core was elucidated using molecu oligonucleotide under nearphysiological conditions lar dynamics simulation; it was shown that migration [25]. occurs predominately via the terminal Gtetrads, and the Considerable structural diversity is characteristic for quadruplex loops affect the process. Location of internal DNA G4s due to such factors as the number of forming cations depends on their size and charge. The distance molecules, length of Gtracts, mutual orientation of between the electronegative oxogroups of guanine strands, base sequence (composition) and length of G4 residues in the Gtetrad decreases when a cation enters loops, availability of oligonucleotide fragments flanking the quadruplex channel, due to electrostatic attraction, the G4motif, type of cations in the medium, and others which prevents the release of cation into bulk solution [26]. G4s can adopt manifold topologies characterized by [30]. different orientation of the four strands in the quadruplex Among monovalent cations, the maximum stabiliz stem. The structure is parallel if all the strands point in the ing effect has been observed for K+, which is located same direction. In antiparallel G4 two of the four strands between two consecutive Gtetrads forming eight coordi point in the same direction (two types are identified – nation bonds with the guanine carbonyl groups (Fig. 1b). “chair” and “basket” differing in the type of loops), and The spaces between the lateral or diagonal loops of the in mixed antiparallel–parallel (3 + 1) G4 three strands quadruplex and the terminal Gtetrad are alternative sites have the same orientation (Fig. 1a). Classification of for binding potassium ions [30]. Sodium ions, which usu DNA Gquadruplexes on the basis of the quadruplex ally localize in the tetrad plane and form four coordina twist angles is presented in [27]. Despite the fact that tion bonds with the guanine residues, exhibit less pro loops do not involve in Gtetrad formation, they play a nounced stabilizing effect [31]. In addition to the ionic key role in the overall folding and stability of G4; quadru radius, the difference in the hydration free energy of the plex loops represent elements of secondary structure and ions is suggested as an explanation for the different effect are the main sources of tensions and limitations in the of K+ and Na+ on the G4 stability. quadruplex structure. Three types of loops are character Ammonium ions were used as NMR probes for iden istic for G4s (Fig. 1c): propeller (doublechairreversal) tification of coordination sites of monovalent ions with + ones connecting Gtracts forming neighboring edges of DNA. It was shown that NH4 could be localized inside the the fourstranded core (arbitrarily they can be defined as quadruplex between neighboring Gtetrads the same as loops connecting “upper” and “lower” Gtetrads); no potassium ions [32]. According to other data [33], ammo inversion of the nucleic acid chain direction occurs in this nium ions are too large to be embedded into the inner cav case; lateral (side) loops connecting neighboring Gtracts ity of the quadruplex without partial opening of Gtetrads. (change of the chain direction occurs); diagonal loops Hence, the type of binding of these ions with G4 depends connecting Gtracts forming opposite edges of the G on the rigidity of the fourstranded structure defined by the quadruplex (change of the chain direction occurs). temperature, and it is controlled by steric limitations of G Formation of one type of loop or another depends on the tetrads and the structure of the loops [33]. It was shown number of Gtetrads, number of nucleotide units between using NMR spectroscopy that thallium and rubidium ions the Gtracts, and their composition, and it is directly are coordinated within the Gquadruplex structure like related to the strand orientation in the quadruplex. K+. Thermodynamic stability of G4 increases with Specific coordination of mono and bivalent cations increasing concentration of monovalent ions in the medi inside the G4 as a stabilizing factor of such noncanonical um [34, 35]. It must be noted that Li+ and Cs+ ions have structures of nucleic acids. Considering that Gquadru practically no stabilizing effect on the fourstranded DNA plexes are formed due to association of four structure because their ionic radius either prevents their poly(oligo)anions, electrostatic interactions are their entry into the quadruplex channel or (if it is too small) main stabilizing factor. However, the ions concentrated remaining there by forming coordination bonds with the

BIOCHEMISTRY (Moscow) Vol. 81 No. 13 2016 GQUADRUPLEXES OF NUCLEIC ACIDS 1605 guanine residues [28]. As recently shown, increasing the third loop [26, 42, 45]. At the same time, in the presence concentration of ions that do not stabilize quadruplexes of Na+ the topology of G4s formed by the same oligonu (Cs+ or trimethylammonium ion) at constant concentra cleotides is much more variable and depends to a greater tion of K+ could result in collapse of G4; this effect was not degree on the G4motif sequence than in K+ solution observed for any other DNA structure [35]. [42]. The Gquadruplex with three dinucleotide loops Ions of bivalent metals also affect the stability and can adopt either parallel or antiparallel folding topology, conformation transitions between different forms of G4. but the parallel one is more energetically favorable [46]. Some of them (Ba2+, Sr2+) have sizes that allow entering The parallelstranded structure prevails in G4 with only the central quadruplex cavity [36] and stabilizing G4 sig one singlenucleotide loop. The type of nucleotide (A, T, nificantly more strongly than monovalent ions. For G, or C) in this loop does not affect the Gquadruplex example, the binding constant of intramolecular antipar topology [42]. It was shown using CD spectroscopy that allel G4 with barium cation is 10fold higher than with within the library of intramolecular DNA quadruplexes the potassium cation [30, 37]. The pronounced stabilizing with loop lengths varying from one to three nucleotides, ability of strontium ions has been explained by their the G4 topology shifts from parallel to antiparallel or strong interaction with the guanine carbonyl groups and mixed when the total length of all loops is larger than five effective screening of the phosphate group charges [38]. nucleotide residues [26]. The fact that the propeller loops Bivalent lead ions also stabilize quadruplexes efficiently contain no more than three nucleotides [26] imposes because, as shown by Xray analysis, they are located steric limitations on the number of Gtetrad layers in the between the planes of neighboring Gtetrads and can intramolecular quadruplex (that is on its “height”) [47, replace K+ and Na+ in the quadruplex structure. Ca2+ and 48]. The number of guanosines in the Gtract does not Na+ can coexist in the G4 core, exchanging their posi necessary correspond to the number of Gtetrads [47]. tions easily because their ionic radii are similar. The Thus, it was shown by NMR spectroscopy that oligonu dependence of the Gquadruplex stabilizing ability of cleotide containing Gtract made from 15 guanosine bivalent metal ions on concentration is bellshaped: 2 residues formed a parallel intramolecular Gquadruplex 5 mM salt solutions initiate G4 formation, while when consisting of three Gtetrad layers and three propeller concentrations are above 10 mM in combination with loops containing guanosine residues [48]. elevated temperature, some ions (Ca2+, Co2+, Mn2+, There is a correlation between the type of G4motif Zn2+, Ni2+, and Mg2+) can cause the quadruplex unfold folding and Nglycosidic syn and anticonformations of ing. Probably this is due to specific interactions of biva guanosines forming the quadruplex core. Four possible lent ions with electron acceptor groups of the guanines conformation sets in the GpG dinucleotide sequence responsible for the formation of Hoogsteen hydrogen within G4 are considered: syn–anti, anti–anti, anti–syn, bonds. Comparative ranking of the degree of G4 stabi and syn–syn. They differ significantly in their energy lization by the mono and bivalent metal ions is as fol parameters due to the different geometry of stacking con 2+ 2+ + 2+ + + + 2+ lows: Sr > Ba > K > Ca > Na , NH4 > Rb > Mg tacts between guanines. The 5′terminal GpG sequence > Li+ Cs+ [22]. The cations, especially the bivalent that assume syn–anti and syn–syn conformations are also ones, initiate conformational transitions between the dif considered in [49]. In these dinucleotides, the 5′end ferent G4 folding topologies. Thus, conversion of hydroxyl group forms Hbonds with N3 of the guanine in antiparallel G4 into parallel one occurs under the action synconformation. When all four strands in the G4 are of Ca2+ [39]. A similar effect is observed for telomeric G4s oriented in parallel to each other, all the guanosines are in when a small amount of KCl is added to Na+ solution. It anticonformation, which is most favorable energetically. was shown recently that the G4 with only two Gtetrad In the case of G4 with other topologies, the syn–anti con layers instead of the usually observed threetetrad struc formation of guanosines correlates with the mutual orien ture becomes the predominant form at extremely low tation of the strands changing both inside the Gtetrad concentration of potassium or strontium ions [22]. cycle and along the quadruplex axis (Fig. 1a). Four According to molecular dynamics simulation, the cation grooves are located on the G4 surface with the width does not initiate the quadruplex formation, but rather sta (narrow, medium, and wide) and distribution of the phos bilizes the preformed structure [30]. phate group charges in the sugarphosphate backbone Factors affecting topology of DNA quadruplexes. The depending on the topology of the fourstranded structures type of loops connecting Gtracts, their length, and base [50, 51]. The parallel intermolecular quadruplex has four sequence represent such factors [4042]. The two or almost identical grooves that are of the same size as the threetetrad G4 with three singlenucleotide loops has minor groove of the DNA duplex. Two narrow and two parallel topology and no other, and all the loops are of wide grooves are formed in the G4 with alternating con propeller type [43, 44]. In the presence of K+, the struc formations anti–syn–anti–syn in each tetrad, while one ture with parallel orientation of all the strands is charac wide, one narrow, and two medium grooves are formed in teristic for the quadruplex with two singlenucleotide the G4 with alternating anti–anti–syn–synconforma loops regardless of the length and base sequence of the tions in the Gtetrads.

BIOCHEMISTRY (Moscow) Vol. 81 No. 13 2016 1606 DOLINNAYA et al. Taking into consideration that there are 26 combina shown that predominantly the eukaryotic genomes are tions of different loops and eight possible types of G enriched with G4motifs. They are distributed nonran tetrads with various sets of syn–anticonformations of domly primarily away from the regions involved in nucle guanosine residues, the number of possible conforma osome formation and in nonmethylated regions [65]. tions even for the quadruplexes formed via intramolecu High frequency of G4motifs is observed within telomer lar folding of one oligonucleotide molecule is very large ic DNA [66] and micro(mini)satellite repeats [67, 68], in [52]. Formation of intermolecular structures further long terminal repeats (LTRs) of retrotransposons [69], in increases conformational diversity of G4s. Additional genes of ribosomal RNA, in regulatory regions of the conformation possibilities emerge due to introduction of genome such as gene promoters [70]; predominately in A, C, or Ttetrads into the quadruplex core, as well as the coding (sense) strand [71], in origins of replication due to formation of more complex planar pentads, hexads, [5, 72, 73], in immunoglobulin switch regions and break heptads, and octads stabilized by Hbonds [53, 54] that point regions of chromosome translocation [74], recom contain other bases along with guanines. bination hotspots [75], intronic sequences [76, 77], CpG Quadruplex associates. Some G4s, especially parallel islands, enhancers, and insulators [78], in mitochondrial ones, are prone to interquadruplex interactions [55]. It DNA [79], as well as in various regions of the transcrip was shown by NMR spectroscopy that two intramolecu tome including sites of alternative mRNA processing, lar parallel Gquadruplexes in K+ solution stuck together splicing [80], 5′ and 3′untranslated mRNA regions [2], due to interactions of 5′end Gtetrads (“blunt” end telomeric noncoding RNA [81], premicroRNA [82], interaction) [43, 56]. Models of quadruplex multimeriza and long noncoding RNA [83]. tion via stacking of 3′3′ and 3′5′end Gtetrads have It was shown using the computational methods that been described [57]. Both intramolecular [43] and inter G4motifs are evolutionarily conserved [84]. The densi molecular DNA quadruplexes can interact with each ty of G4forming sequences is significantly higher in the other; moreover, the contact between the G4 subunits can noncoding regions compared with coding ones [85]. be formed not only by the Gtetrads, but also by heptads There are more than 376,000 G4motifs in the human and octads with large hydrophobic surface [53, 54] that genome according to the QuadParser algorithm. More contain different bases in addition to four guanine than 40% of genes encoding human proteins contain at residues. Another type of dimeric G4s is formed similarly least one G4motif in the region [62]. On aver to the assembly of DNA duplexes via “sticky” ends. age, the distribution density of such sequences along the “Sticking” together of two Gquadruplexes can occur due human genome is 0.153 per 1000 base pairs (bp), while to guanosine residues from each subunit participating in their content in promoter regions is 1.48. The maximum formation of new Gtetrad at the two quadruplex subunit on the distribution probability curve of G4motifs in junction. This is what happens during intermolecular human, mouse, rat, yeast, and E. coli genomes corre assembly of G4 by four molecules of the d(GGGT) sponds to a site located at approximately 50 bp from the oligonucleotide. The Gtracts of the initial G4 slide along transcription start site (TSS). On the other hand, more each other providing the dimer formation. The design of than 800 G4motifs are localized in regions removed oligonucleotide constructs for formation of Gquadru from the TSS of 22,049 human genes by up to 5000 bp plex structures of higher order has been described [58]. [86, 87]. The fact that G4forming sequences were evo lutionarily conserved support the role of DNA G quadruplexes in key cellular processes [88]. The gene LOCATION OF GQUADRUPLEXFORMING regulatory regions of warmblooded animals are more SEQUENCES IN GENOMES enriched with G4 motifs [80], with the human genome AND TRANSCRIPTOMES containing the highest number. Moreover, the presence OF VARIOUS ORGANISMS of G4motifs has been observed equally in regulatory sites of early and late genes. In general, they precede The main strategy for genome analysis involves cor oncogenes and less often tumor cell suppressor genes rect determination of sequences that can be assigned to [89]. The G4motifs are mostly associated with genes G4motifs. The set of sequences that were shown experi encoding proteins responsible for regulatory functions mentally to form Gquadruplexes is considered as a basis rather than “housekeeping” proteins. Homology set [59]. Algorithms for searching and marking of G4 between G4motifs of vertebrates and yeasts in the mito forming sequences have been developed in the last decade chondrial and nuclear genomes was revealed by compar due to accumulation of a large amount of data on ative in silico analysis [85]. Interestingly, there is one sequencing of genomes of mammals and bacteria [60, order of magnitude more G4motifs in the mitochondr 61]. The distribution of G4motifs revealed by the ial DNA from S. cerevisiae than in the nuclear genome

QuadParser algorithm (GnL17GnL17GnL17Gn, where n [90]. In plants, quadruplexforming sequences acting as 3, L = A, T(U), G, C) in the genomes of different organ translation repressors were found in 5′untranslated isms was investigated in several works [6264]. It was regions (UTR) of mRNA [91]. Retrotransposon LTRs,

BIOCHEMISTRY (Moscow) Vol. 81 No. 13 2016 GQUADRUPLEXES OF NUCLEIC ACIDS 1607 which are highly abundant in plants, contain a large eukaryote (ciliate) Oxytricha nova – (TTTTGGGG/ number of G4motifs [69]. CCCCAAAA). False negative and false positive G4motifs. G4motifs in bacterial and viral genomes. The distri Numerous regions have been elucidated in recent years in bution of G4motifs in the genomes of these species is still the human genome with primary structure deviating from poorly understood. The implication of G4s in virology the GnL17GnL17GnL17Gn pattern (where n 3, L = A, only begins to be realized. In the E. coli genome, they also T(U), G, C), which nevertheless form quadruplex struc are mainly located in regulatory regions, which suggests tures [92]. The G4motif within minisatellite DNA that participation of G4s in regulation of transcription [98]. folds into a quadruplex with 9nt middle loop is consid The search for Gquadruplexes and elucidation of their ered as a false negative [67]; the dominating G4 formed functions in viral genomes has mostly focused on the HIV in the promoter of the human Bcl2 gene assumes paral retrovirus. Location of G4motifs near recombination lel topology with a 13nt loop [87]. According to other hotspots, central polypurine tract at the 3′end of the pol data, the average middle loop of a stable G4 can contain gene, and in HIV1 LTR promoter indicates participation up to 21 nucleotide residues [93]. Moreover, recently the of G4s in recombination, replication, and regulation of evidence was presented for occurrence of bulges (that is HIV1 promoter activity [99101]. It has been suggested the incorporation of nonguanine bases in Gtracts) in that G4s formed close to the origins of replication within different G4 contexts. It was shown using NMR spec DNAcontaining Epstein−Barr virus play an important troscopy and other methods that single or multiple bulges role in DNA replication and metaphase chromosome in the quadruplex core can vary in length, nucleotide attachment [102]. Moreover, it was shown recently that composition, and location [94]. There are also data of G4 clusters were responsible for regulation of virus falsepositive G4motifs that obey the classical pattern encoded nuclear antigene 1 mRNA translation [103]. The but do not form quadruplexes. Thus, Grich sequences in G4motifs presented in the noncoding regulatory DNA 5′UTR of human mRNA were not able to fold into region of the SV40 virus can form unusual structures with quadruplexes due to the availability of Ctracts in flank a Ctetrad integrated into the quadruplex core. It was ing regions, which hybridized with the Gtracts forming suggested that these quadruplexes play an important role alternative secondary structures [14]. To overcome these in the regulation of replication as well as early and late limitations, other more accurate tools to predict G4 transcription of the viral genome. The G4forming propensity of a given DNA or RNA sequences are need sequences and their potential to form quadruplex struc ed. More general criteria should be taken into account, tures were analyzed in the genomes of all known human for example, the effect of neighboring sequences, which papillomaviruses [104]. Participation of G4s in transcrip could cover wider functional regions of genomes and tion, replication, and alternative splicing required for transcriptomes [95, 96]. Development and testing of a production of viral proteins has been discussed for at least radically different algorithm, G4Hunter, was suggested in some of them. The role of Gquadruplexes in the life 2016. This algorithm takes into consideration Grichness cycle of viruses, such as HIV, as well as applications of and Gskewness (G/C asymmetry between the comple G4containing DNA aptamers as antiviral agents, diag mentary strands of the double helix) of a given sequence nostics, and innovation tools have been discussed [43, [97]. To validate the G4Hunter, a large dataset was ana 105]. lyzed, and G4forming potential for human mitochondr ial DNA fragments was evaluated using the combination of biophysical methods. Analysis of genomes of various METHODS USED FOR G4 ANALYSIS in vitro; organisms using the developed algorithm showed that the THERMODYNAMICS AND KINETICS number of sequences capable of forming stable G4s in the OF QUADRUPLEX FOLDING–UNFOLDING human genome is significantly (210fold) higher than estimated before. To characterize Gquadruplexes formed in a certain G4motifs at the ends of eukaryotic linear chromo genome locus, each identified G4motif is investigated in somes (). It is known that telomeric DNA con vitro under different experimental conditions close, to a sists of tandem repeats of G⋅Crich noncoding sequences lesser or greater degree, to the intracellular ones. The with a 150250nt singlestranded Grich overhang at the methods commonly used for the description of G4 topol 3′end. In human cells as well as in the cells of all verte ogy and determination of thermodynamic and kinetic brates, telomeric DNA comprises a (TTAGGG)/(CCC parameters of Gquadruplex folding and unfolding TAA) repeat with size of several thousands of base pairs. include CD [106, 107] and UVspectroscopy [108, 109], Similar G⋅Crich repeats are characteristic for many phy differential scanning calorimetry [110, 111], gel elec logenetically distant species; the typical telomeric trophoresis [29, 52], Xray crystallography [25, 112], sequence in insects contains the (TTAGG)/(CCTAA) chemical and enzymatic probing [101, 113, 114], fluores repeat, in plants – (TTTAGGG)/(CCCTAAA), in cence spectroscopy, fluorescence resonance energy trans Tetrahymena – (TTGGGG/CCCCAA), and in the lower fer (FRET) [34, 46, 115, 116], including single molecule

BIOCHEMISTRY (Moscow) Vol. 81 No. 13 2016 1608 DOLINNAYA et al. FRET [41, 117, 118], Raman spectroscopy [119], elec site (in one or different Gtetrads) is also reasonably sta tron paramagnetic resonance [120, 121], hydrodynamic ble [134]. Furthermore, G4 with a single apurinic site can and chromatographic techniques [52], molecular model be formed by other sequences, such as human telomeric ling and molecular dynamics simulation [30, 122124], repeats [135]. It is interesting that “excess” of guanosines massspectrometry [125], and NMR spectroscopy [56, in some Gtracts can cause their sliding relative to each 126, 127]. The detailed characteristic of several methods other during formation of quadruplex structures. It was used for G4 investigation have been described [128]. shown that this process stabilized the folded state; the Tm A large amount of data is available in the literature value of G4 increased significantly due to favorable on the kinetics and thermodynamics of G4 formation that entropic changes [136]. were obtained using traditional approaches [128]. Factors affecting thermodynamic parameters of G4 However, unlike Gquadruplex structure, these aspects folding–unfolding. Among these factors, the cation com have not been studied systematically. Also, correlation position and ionic strength of the buffer solution, number between the thermodynamic stability, kinetics, and G4 of interacting molecules, their primary structure, and structures has not been considered. Typically, the thermo length of Gtracts [109], as well as the presence of dynamic parameters of individual G4 folding–unfolding nucleotide fragments flanking G4motif [137] have been were investigated and usually by different methods [129]. studied. The stability of G4 depends strongly on the type An algorithm for predicting quadruplex stability was of loops, their length, and base composition/sequence developed based on nonsystematic data [130]. [93, 138]. Replacement of only one base in a one or two Spontaneous folding of singlestranded sequences con nucleotide loop of a quadruplex and in the G4flanking taining Gtracts into quadruplexes is a thermodynamical fragments can affect G4 stability [42, 137, 139]. In par ly favorable process [128]. Unlike other noncanonical ticular, the replacement of T or C by A in the one structures, Gquadruplexes are formed under conditions nucleotide loop of parallel G4 with (1:3–9:1) loops caus close to physiological, and their melting temperature es significant destabilization of the quadruplex structure

(Tm) can exceed 7080°C. Of critical importance for the [42]; according to NMRspectroscopy data, the adenine stabilization and unfolding paths of G4s, not found in residue is pushed out of the G4 groove, unlike the DNA and RNA duplexes, are the cations within the cen thymine residue, which is in the quadruplex groove [140]. tral quadruplex channel. The ΔG° and ΔH° values of It was shown that independent of the orientation of DNA intramolecular G4 formation from 2226nt sequences strands, the thermodynamic stability of intramolecular (34 Gtetrads) in 100 mM K+ vary in the range from –2 G4 decreased with increasing length of loops [26, 93, to –8 kcal/mol and from –30 to –80 kcal/mol, respec 139]. Indeed, each additional nucleotide in a propeller + tively; the stability of Gquadruplexes in Na solution is loop decreases the Tm value by 2°C [42, 93]. This depend significantly lower [31]. Unlike G4, the stability of DNA ence is not connected with the base sequence in the G4 and RNAduplexes does not depend on the type of loops; this was shown using a set of threetetrad intramol monovalent cations. Analysis of the thermodynamic data ecular Gquadruplexes with partially randomized loop has shown that intramolecular G4 are not more stable sequences [26]. In the case when the total length of all than other intramolecular complexes of nucleic acids loops exceeds five nucleotide residues, its further increase [128]. Hairpin DNA structures exhibit significantly high affects the thermodynamic stability only insignificantly. er Tm value than G4s of comparable length under equal On the other hand, Hbonds or stacking contacts in long conditions [131]. It was also shown that in most cases the quadruplex loops [141], as well as stacking interactions of energy of G4 formation is not sufficient to separate the loop bases with terminal Gtetrads, could provide favor strands of double helix (>20 bp) in inner DNA sites such able contribution of enthalpy to the thermodynamics of as promoter regions [128]. However, special properties G4 formation. The stability of G4 also increases when the have been assigned to intramolecular parallel G4 formed bases in the long loop can hybridize with the bases of the by the d((GGGT)3GGG) sequence; folding of this G4 5′end sequence flanking the G4motif [142]. structure is much more energetically favorable than for It is known that the G4 formation is accompanied by mation of the DNA duplex in the presence of comple the release of water molecules [143]. The thermodynam mentary strand [132]. Moreover, the replacement of ic contribution of dehydration and capture of counter guanosine in the first Gtract (at the second position) by ions was estimated in [50]. It was shown that water affect an apurinic site does not prevent folding of the analogous ed thermodynamic stability and polymorphism of G4s sequence into G4, although it results in significant desta [110, 144]. The decrease in water activity caused by addi bilization of the structure [133]. It was shown by molecu tion of various alcohols or polyethylene glycol (PEG) into lar dynamics simulation that the vacant place in the aqueous solution, results in stabilization of the quadru formed Gtriad is occupied by a water molecule. The plex [145]; PEG is usually used as molecular crowding unique binding pocket in G4 can be used as a specific tar agent to create cellmimicking conditions. It should be get for low molecular weight ligands and nucleic acids noted that the solvation effects observed for intramolecu metabolites. The G4 containing more than one vacant lar quadruplexes and DNA double helices are diametri

BIOCHEMISTRY (Moscow) Vol. 81 No. 13 2016 GQUADRUPLEXES OF NUCLEIC ACIDS 1609 cally opposite; decrease in water activity destabilized B whose interaction initiates formation of the quadruplex DNA, but increased the stability of G4 [131]. However, core, or these can be Gtriplexes varying in topology that the effect of PEG causing dehydration of quadruplexes on are formed via separation of one of the Gtracts from the their stability is not so unambiguous. As shown in 2016, quadruplex [153]. The evidence for the occurrence of the G4 stability in the presence of monovalent ions these structures stabilized by Gtriads was obtained increased after addition of molecular crowding agents. In experimentally by NMR and CD spectroscopies, differ contrary, PEG stabilized only parallel G4s, but had no ential scanning calorimetry, and other techniques [134, effect on stability or even destabilized antiparallel or 149], and the properties of possible Gtriplex forms were mixed G4 structures in the presence of bivalent ions analyzed by molecular dynamics techniques [154]. It was [143]. According to a suggested hypothesis, Sr2+, Ba2+, shown that the number of intermediates determined the and Pb2+ compensate to some degree the effect of dehy kinetics of fullsized G4 folding. The number of these dration accompanying formation of G4 structure, espe states observed in K+ solution was less than in Na+ buffer cially in the case of Gquadruplexes with antiparallel ori [155]. The fundamental difference in the behavior of par entation of strands. allel G4 with all guanosines in anticonformation, which The most detailed and comprehensive information is allowed slippage of Gtracts along each other with forma available on the thermodynamics and kinetics of tion of intermediates with lower number of Gtetrads in intramolecular G4 formation by oligonucleotides con the quadruplex core, and antiparallel G4, in which the taining four Gtracts from human telomeric DNA repeats syn or anticonformation of guanosine residues correlat [109, 128, 130]. The thermodynamic data for oligonu ing with the strand directions blocked the slippage cleotide models with identical or similar primary struc process, was specifically emphasized. It is of interest that ture were summarized in a review published in 2010 the number and type of residues attached to 5′ and to 3′ [129], where the presented ΔG° values varied over a wide ends of the G4 affect the rate of quadruplex formation, range (3.414.8 kcal/mol). The reasons for the observed but they do not change its multistep mechanism. parameter variation were associated with polymorphism The kinetics of Gquadruplex folding depends on the of telomeric DNA quadruplexes. It is now recognized base sequence of the G4motif and varies in the range that most G4motifs can form Gquadruplexes of differ from milliseconds to minutes. It was noted that the time ent architecture that are energetically similar and at of G4 formation of human telomeric repeats that were dynamic equilibrium. Various types of G4 conformations capable of very fast intramolecular folding correlated with can be formed at different rates, which results in non the time of DNA replication [156]. According to data identical sets of conformers under variant conditions of obtained using various experimental approaches, high sample preparation and using different investigation rate of telomeric G4 folding (1650 s–1) was observed at methods [146]. But even under the same conditions the low concentrations of potassium ions (<10 mM), while identical telomeric sequence can fold into many different the rate of their unfolding was low (1.3·10–3 s–1) [128, quadruplex structures [109], and the formed G4 can con 155]. Unusually slow melting of intramolecular quadru vert into other conformations that are separated by only plexes was also postulated [157]. The statement on the slight energy barriers (2 kcal/mol) [147]. It was shown high folding rate of the Gquadruplex structure contra that individual conformers could be almost identical in dicts the results of theoretical analysis [158], according to thermodynamic, electrophoretic, and hydrodynamic which competition between the different conformations properties, but exhibit different CD and NMR spectra as of Gquadruplexes including the intermediates (especial well as kinetic stability [52]. ly DNAhairpin structures) makes this multidirectional Controversial opinions have been presented in the process very slow. In the view of authors, the G4 forma papers regarding whether the intramolecular folding– tion follows a very complex kinetic pathway involving unfolding of the single G4 is a simple onestep process. It multiple alternative states, and only a small fraction of has been advocated in some publications that G4 melting molecules is folded into the final G4 structure. Data proceeds according to a twostate model [111]. However, obtained recently by NMR [159] and CD [110] agree most researchers believe this process proceeds via inter with such kinetic pattern. mediate stages and does not correspond to an “allor Regarding intermolecular G4s, the polymorphism of none” model [129, 148, 149]. Using CD spectroscopy, these structures is defined by kinetics limitations even fluorescence assay, and FRET, a multistep mechanism of more than in the case of intramolecular G4s. Kinetic telomeric G4 folding was verified recently, and the kinet models that differed significantly depending on the type ics of each step was investigated [150, 151]. According to of the cation (K+ or Na+) in the environment were sug data of biophysical, computational, and other methods, gested in a work of Prislan et al. [160] based on tradition G4 formation proceeds via thermodynamically and al approaches. These models describe the processes of G4 kinetically significant intermediates even during intra folding–unfolding and structural transitions between the molecular folding of the oligonucleotide [149, 152]. different quadruplex conformations formed by the

These intermediates can comprise hairpin structures d(G4T4G3) oligonucleotide with two Gtracts.

BIOCHEMISTRY (Moscow) Vol. 81 No. 13 2016 1610 DOLINNAYA et al. Potential of singlemolecule techniques for Gquadru ation of singlestranded Grich repeats (telomeric DNA plex study. The commonly used experimental methods or promoter fragments) sandwiched between long pulling allowing exploring averaged properties of a multitude of doublestranded DNA (dsDNA) handles immobilized on molecules (CD, NMR spectroscopy, Xray crystallogra two opticallytrapped or paramagnetic beads [146, 153, phy) are not so informative for the analysis of distinct G4 157, 161, 162]. According to [163], unwinding of struc structures, especially those comprising a small fraction tured DNA under stretching is physiologically more within heterogeneous population. Investigation of behav rational that thermal melting, the latter being impossible ior of single molecules provides more information for in vivo. On the contrary, DNA replication, transcription, determination of the subpopulations of various structures and other processes can stretch DNA, which causes local in polymorphic mixture. For instance, the structure and unwinding of the double helix. The mechanical stability of dynamics of G4 at the single molecule level was investigat G4s was evaluated using optical tweezers, and it was found ed using FRET, and the coexistence of several types of to be comparable with the force causing the stop of DNA quadruplex conformations formed by human telomeric and RNApolymerases. Comparative study of mechanical repeats was revealed [117]. In recent years, the original stability of G4 and the hairpin DNA under physiological laser and magnetic tweezers were developed for investiga conditions using the same technique revealed that unlike tion of thermodynamics and kinetics of conformational the hairpin structures, DNA quadruplexes could serve as transitions that occur due to mechanical stretching–relax an efficient barrier for replication or transcription [164]. It

a

b

c 1Htetrazole CH2Cl2

Solidphase Alkyneazide DNA synthesis cycloaddition

Fig. 2. Direct quantification of loop interactions and Gtetrad stacking using the optical tweezers and chemical approaches. Assisted by click chemistry, pulling dsDNA handles were attached via two modified guanines in each of the three Gtetrads. The G4 is presented on the scheme with “upper” or “lower” tetrad covalently bound to the DNA duplexes (a, b). Attachment of the dsDNA fragment carrying an azide group (4) to the guanosine derivative of the G4motif with an alkyne group in the adjacent phosphate residue (3) was conducted via alkyneazide cycloaddition (5). The modified guanosine residues after introduction of the alkyne group to the 3′end phosphate (1) were used as synthons (2) in solidphase oligonucleotide synthesis. This allowed introducing alkynecontaining residues to predetermined positions of the Grich oligonucleotide (c). A similar strategy was used for attachment of dsDNA to Gquadruplex loops. The laser beams focused onto beads are pre sented as yellow cones.

BIOCHEMISTRY (Moscow) Vol. 81 No. 13 2016 GQUADRUPLEXES OF NUCLEIC ACIDS 1611 was shown using molecular dynamics simulation that the helix is the native context for genomic DNA. The fluores unfolding event of intramolecular G4s of different topolo cence assay in a combination with G4recognizing low gy under mechanical stretching was accompanied by the molecular weight ligands was used to measure the G4 loss of coordination between the central ion and guanines folding propensity in both singlestranded and double of the Gtetrads [165], which agreed with experimental stranded DNAs [116]. As expected, the ability of G4 data [166]. motif to form G4 was substantially diminished in the In pioneering work [167], new strategy was devel DNA duplexes due to the competition from the oped to discriminate the contribution of loops and G Watson–Crick base pairing. Unlike G4 folding sequence tetrad stacking to quadruplex stability at the force in singlestranded DNA, which forms both parallel and induced G4 unfolding. The contributions from G4 ele antiparallel G4s, dsDNA displays only parallel folding. It ments were determined using optical tweezers technique was shown in several studies that G4–DNAduplex equi and click chemistry (Fig. 2). Mechanical unfolding of librium depended on many factors affecting relative sta human telomeric G4 revealed that the loops’ interactions bility of both secondary structures: temperature, avail contribute more to the G4 stability than the stacking of ability of fragments flanking G4, primary structure of G Gtetrads. motif, cationic composition, and other factors. One such The use of magnetic tweezers allowed characterizing factor is the length of loops in the quadruplex; the short the equilibrium conformational transitions in intramole er they are, the more stable is the G4 and, consequently, cular telomeric G4 at physiological concentrations of the less stable is the duplex formed in the presence of potassium ions (∼100 mM) [146], which was impossible complementary strand due to the shorter hybridization to do using optical techniques due to the high stability of site [116]. Thus, oligonucleotide with human telomeric quadruplexes under these conditions. Three quadruplex repeats d(TTAGGG)4 (the length of loops in the G4 conformations were revealed in a timeframe of several structure are 3 : 3 : 3) forms duplex under physiological minutes, which exhibited different lifetimes and mechan conditions in the presence of complementary Crich ical stabilities. It was shown that the kinetically controlled strand, while the sequence of the Cmyc promoter distribution of human telomer DNA G4 isomers depend d(GGGTGGGGAGGGTGGG) predominantly assumes ed on conditions of their formation [168]; in other words, G4 conformation with 1 : 2 : 1 loops. The same factor – the longerlived and more thermodynamically stable iso change in length of the hybridization site – shifts the mers could be accumulated in a sample with increasing equilibrium towards the duplex formations in the case of experiment duration. The magnetic tweezers technique the G4motif flanked with nucleotide residues [169]. was used to study the kinetic properties of G4 formed Similar regularities were observed during monitoring of from a 27nt Grich region of the oncogene cMyc pro isothermal G4 unwinding in the presence of complemen moter at 100 mM K+. The dominating G4 conformation tary strand carrying fluorescent label [170]. It was shown was shown to melt more slowly by several orders of mag that availability of the sequence neighboring the G nitude than Gquadruplexes of other topologies [157]. It quadruplex accelerated this process approximately two was suggested that this noncanonical structure could fold, and the K+ concentration was found to be a key fac play a role of a kinetic barrier in transcription regulation. tor controlling the kinetics of G4 unwinding in the pres Analysis of the published data indicates that the ence of a complementary strand. Thus, the G4 formed by paths of G4 folding–unfolding and their thermodynamic the Cmyc promoter sequence remains stable in the pres and kinetic parameters can vary for different quadruplex ence of the complementary strand even at 70°C in es and different experimental conditions. It is likely that 100 mM KCl. If the G4motifs potentially can fold there is no universal mechanism appropriate for all G4s intramolecularly into imperfect hairpin duplex as in the and sample preparation conditions. But the combination case of the promoter region of the WNT1 gene, of modern experimental techniques and advanced com d(GGGCCACCGGGCAGGGGGCGGG), the K+ putational methods could help to elucidate which induced transition into G4 occurs significantly more quadruplex conformations are most represented on bio slowly than the quadruplex formation from the unstruc logically significant time scales. tured oligonucleotide [171]. Addition of PEG, which decreases water activity, facilitates G4 assembly even in the absence of cations and shifts the equilibrium from the FACTORS AFFECTING DNADUPLEX– DNA duplex formed by the telomeric repeats with the GQUADRUPLEX–iMOTIF EQUILIBRIUM complementary strand to G4. The use of complementary probes with enhanced hybridization ability, for example Besides telomeric ends, G4forming sequences are peptide nucleic acids (PNA), on the contrary results in present in the genome together with complementary effective G4 unfolding and formation of a heteroduplex strands in the form of double helix. Thus, investigation of (DNA/PNA) [172]. thermodynamics and kinetics of the equilibrium between The DNA double helix in vivo becomes temporarily G4 and duplex DNA is important because the double singlestranded during replication, reparation, and tran

BIOCHEMISTRY (Moscow) Vol. 81 No. 13 2016 1612 DOLINNAYA et al. scription, and the open forms can later fold into various (Fig. 3). The factors that affect the stability of imotif noncanonical structures. The conformational rearrange (pKa value, length of loops, epigenetic modification of ment of duplex DNA into G4, for instance, in gene pro cytosine residues, presence of PEG, degree of hydration) motors, can be reached through supercoiling effect. It is were recently analyzed [178, 179]. Oligonucleotides with known that the transcription machinery can generate Grich and Crich sequence from the gene promoters negative supercoils behind the moving RNA polymerase. were shown in in vitro experiments to fold into Gquadru Negative superhelicity stimulates G4 formation [86], plexes and imotifs, respectively, under certain condi because the local unwinding of duplex DNA is facilitated tions. The competition between two types of fourstrand under conditions of topological stress, thus relieving the ed structures and DNA duplex depended on the cation superhelical constraints. The effect of supercoiling can composition and pH of the medium. Distancedependent propagate along the double helix of chromosomal DNA DNA duplex destabilization caused by proximal G4 or i over large distances, initiating conformational rearrange motif structures was estimated [180]. This rather artificial ments of genome sites separated by several thousand base model comprises a fragment of double helix with protrud pairs from the TSS [86]. That is why not oligonucleotide ing singlestranded end, which folds into one of the non models but supercoiled plasmids containing inserts of canonical forms. Though the slightly acidic medium sta doublestranded G·Crich DNA with Gtracts on one of bilized the imotif [176], the formation of this alternative the strands and Ctracts on the complementary one are structure occurred even at neutral pH under conditions of better for modeling in vivo conditions. It was shown using DNA supercoiling [113] or in a molecular crowding envi these models that G4 can exist inside a duplex DNA that ronment imitated by adding of special reagents [181, is the native genomic context [113, 173]. They are formed 182] – two physiologically relevant states of the genome. much more easily in the case of negative supercoiling that There are contradicting data on whether an imotif is before the transcribed sequence but not behind it [86]. can be folded in the complementary singlestranded The statistical mechanism of transitions from BDNA to region after a G4 is formed in the opposite strand, or they G4 includes competition between the two states, and the are mutually exclusive. On one hand, formation of G equilibrium distribution between them at a certain level of quadruplex and imotif in the promoter regions of the c negative supercoiling is calculated from values of free Myc gene inserted into the supercoiled plasmid (Fig. 3c) energy for alternative conformations [174]. Modern tech was established using chemical footprinting [113]. It was niques of magnetooptical tweezers that combine the found that the G4 and imotif were slightly displaced rel nanometer resolution with the possibility to generate the ative to each other (contain only three common G·C prescribed level of DNA supercoiling by a pair of magnets tracts from the four required); moreover, a longer DNA were used for quantitative evaluation of the relationship fragment was used for formation of imotif, because, between the degree of topological stress and the efficien unlike Gquadruplex, long loops increased the stability of cy of Gquadruplex formation. It was shown that the G4 the fourstranded Crich structure [70]. On the other population increased from 2.4 to 23% with increase in the hand, it was shown using the laser tweezersbased single density of negative supercoiling to –0.05; moreover, the molecule technique and chemical footprinting approach G4 formation efficiency correlated with the readiness of [163] that the fragment of double helix that contained the the DNA double helix melting [175]. In addition to G⋅Crich region (ACAGGGGTGTGGGC)2/(GCCCA supercoiling, the structure of chromatin, binding of pro CACCCCTGT)2 from the insulinlinked polymorphic teins specifically recognizing quadruplex structures [4], region (ILPR) formed only one fourstranded structure, and the effect of molecular crowding [116] can mediate a but not both, under conditions that favor the formation of shift of equilibrium from DNA duplex to G4 in vivo. G4 and imotif – pH 5.5, 100 mM K+. Formation of only It was shown using oligonucleotide models and plas one of the quadruplexes in this site was attributed to mid constructs that the intramolecular folding of Grich mutual steric hindrances emerging due to the mechanical sequences into the G4 could be accompanied by the for stretching–relaxation of the dsDNA. A more general mation of noncanonical fourstranded imotif by com conclusion was suggested in a study conducted in 2016, plementary the Crich strand (Fig. 3) [70, 113, 176, 177]. where the formation of G4 and imotif in different frag The enzymatic and/or chemical footprinting experiments ments of doublestranded DNA (human telomeres and are usually used to provide direct insight into the G4 and gene promoter regions) was investigated using the optical imotif folding patterns because these purinerich/pyrim tweezers technique and population analysis. It was shown idinerich tracts are the nucleasehypersensitive regions that mutually exclusive formation of one of the quadru [113]. They are considered as markers of Bform distor plexes was the consequence of steric hindrance in duplex tions, such as “unwound” regions and various non DNA; thus, simultaneous formation of both quadruplex canonical structures. It is known that the pHdependent es separated in the complementary strands was observed imotif structure is formed by two parallel duplexes stabi in the Bcl2 gene promoter [183]. The variability in for lized by semiprotonated C≡C+ pairs (Fig. 3a) through mation of fourstranded noncanonical DNA structures their intercalation in mutually antiparallel orientations governed by appropriate base sequence can facilitate fine

BIOCHEMISTRY (Moscow) Vol. 81 No. 13 2016 GQUADRUPLEXES OF NUCLEIC ACIDS 1613 a b c 5′ 3′

Fig. 3. Fourstranded imotif formed by Crich strand that is complementary to G4forming sequences. Semiprotonated C≡C+ pairs (a) sta bilizing parallel duplexes whose mutual intercalation results in formation of imotif with the C≡C+ pairs being in different planes (b). Two types of fourstranded structures formed by G/Crich sequence integrated into DNA plasmid; G4 is shaded with green, and imotif – with yellow (c).

tuning of gene expression [184], because the G4 forma motif [189, 190]. It was shown using the thrombinbind tion represents the signal for inhibition of transcription, ing aptamer as an example that both duplex and antipar while the imotif can play a role as the activation signal allel Gquadruplex domains coexist in intramolecular [177, 184]. structure of aptamer. The interrelationship between the Oligonucleotide DNAmodels with coexisting duplex duplex and Gquadruplex domains was identified: and Gquadruplex domains. In recent years, oligonu destruction of one via sitedirected modification of cleotide systems containing G4duplex hybrids of various oligonucleotide sequence resulted in dissociation of the topology have attracted considerable attention [185]. other [190]. The 3D structure of an aptamer with similar Investigation of thermodynamic stability of constructs base sequence was investigated by Xray crystallography with contrasting orientations of the duplex stem with [112]. Formation of the duplex domain was not observed respect to the G4 core (coaxial or orthogonal) (Fig. 4) when the mutually complementary sequences flanked the showed that in the case of the structured long loop, the parallel G4 because in this case the complementary frag stability of the quadruplex increased; furthermore, the ments were separated in space; their existence only desta type of the base pair closest to the duplexG4 junction bilized the G4 structure [44]. and the availability of bulges at the boundary of two domains affected significantly the stability of the formed secondary structure [186]. As shown by NMR spec troscopy, stable structures were formed also in the case of a b multiple duplex stems within the same loop of the paral lel G4. Moreover, the multiple duplex inserts could be located in different loops of the same G4, allowing wider variety of the architecture of these structures [187]. The availability of sequences capable of folding into G4 with double helix in one of the loops (with length up to 20 nucleotide units) was analyzed in 2015 [188]. A large number (80,307) of duplex stemloopcontaining G4 motifs organized as clusters was identified in the human genome: in the hotspots of mutations and in the promot er regions of genes associated with oncological diseases Fig. 4. DNA aptamers that have coexisting structures of G4 and and brain tissue pathogenesis. It was suggested that this duplex localized in one of the G4 loops (base pairs are marked type of twodomain structure can participate in various with pink). The construct (a) involves the orthogonal orientation of the duplex and the parallel G4 with no base stacking between biological processes including pathological ones. two domains. Construct (b) involves coaxial orientation of the In other types of duplex–G4 hybrids, complementa duplex and Gquadruplex helices with continual base stacking ry sequences were attached to the 5′ and 3′ends of a G4 across the two domains.

BIOCHEMISTRY (Moscow) Vol. 81 No. 13 2016 1614 DOLINNAYA et al. STRUCTURAL ORGANIZATION garland depends on the number of Gquadruplex units OF MULTIQUADRUPLEXES FORMED [201]. The authors proved that the observed decrease BY NUCLEIC ACIDS WITH MULTIPLE GTRACTS in the stability of the structure formed by d((GGGT

TA)4m–1GGG), where m = 2, 3, 4, with increase of the Simple singlequadruplex models are now replaced number of G4 units, was related to the fact that the G4 at by more biologically relevant multiquadruplex models, the 5′end of the molecule was more thermodynamically which provide the possibility for investigation of interac stable than the G4 at the 3′end, whose stability in turn tions between G4 subunits [56, 191]. Conformation was higher than the stability of the inner quadruplex potential of long singlestranded DNA and RNA with domains. In other words, the stability of individual G4 in human telomeric repeats, which allow the folding of more the garland is modulated by the flanking nucleotide sites. than one G4, was mostly investigated [111, 192194], as Thus, each inner G4 is surrounded by the TTA sequence well as that of several other sequences from the human from both sides, while the terminal G4 – only from one genome that contain many Gtracts arranged in tandem, side (Fig. 5a). The validity of this explanation has been such as gene promoters [195], insulinlinked polymor confirmed by results of investigation of long G4motif phic region [193], minisatellite loci CEB25 [67], and flanked with trinucleotide sequence TTA: d(TTA microsatellite repeats [196]. (GGGTTA)4m–1GGGTTA), where m = 2, 3, 4. It was Two models were experimentally confirmed for found that the overall stability of the multiquadruplex structures with multiple G4s: “beadsonastring” [67, structure formed by this oligonucleotide did not depend 192194, 197], in which the individual G4s are separated on the number of G4 units, because in this case both the by singlestranded fragment and behave independently inner and terminal G4 were flanked with trinucleotide from each other, and a model in which G4 are in contact sequences from both sides (Fig. 5b). It is of interest that with each other, interacting and forming higher order these results do not change with varying length of the structures [111]. Furthermore, interaction of neighboring fragment flanking G4. G4 occurs not only via stacking of terminal Gtetrads, At the same time, the higherorder Gquadruplex but also via loop bases, which results in formation of rigid ensembles are significantly more stable than the individ superstructures. Conflicting opinions have been expressed ual G4s, and the interquadruplex interactions represent based on investigation of long telomeric DNA and RNA the stabilizing factor in this case [196]. by Xray analysis, NMRspectroscopy, and massspec trometry methods regarding the model corresponding to structural organization of sequences with multiple G SMALLMOLECULE LIGANDS AND PROTEINS tracts [56, 111, 125, 191]. These contradictions could be RECOGNIZING AND SPECIFICALLY BINDING explained by structural polymorphism of neighboring G GQUADRUPLEXES quadruplex units and availability of intermediate and defective structures formed during G4 folding [153, 198]. Conformational features of G4s, which are funda It was suggested in several papers that both types of struc mentally different from the other structured DNAs, rep tures (“beadsonastring” and interacting G4 subunits) resent a basis for molecular recognition of Gquadruplex could coexist in long telomeric DNA or RNA, and their structures by low molecular weight ligands. Hundreds of ratio depended on various factors in the cell. small molecules of various chemical nature that are capa It was shown for simpler models that oligonu ble of selective interactions with G4 have been produced cleotides containing more than four guanosine tracts and investigated in the last two decades [202]. They can formed several Gquadruplexes by using various combi recognize either preformed Gquadruplexes [203] or ini nations of Gtracts (position isomers) [52, 199, 200]. It tiate folding of the G4motifs into such structures. The was shown that the sequences capable of forming two small molecules that bind and stabilize G4s in telomeric individual G4s separated by oligonucleotide linker of var DNA and oncogene promoters are considered as poten ious length could fold via different means [199]. tial antitumor agents [8, 77]. Moreover, G4 ligands are Predominately one Gquadruplex is formed if the linker invaluable tools for investigation of the biological role of is short (number of nucleotide units “3) and is found at Gquadruplexes [204], as well as for their detection and different positions along the oligonucleotide chain isolation from cells [205207]. Numerous articles and (entropy gain), while in the case of longer linker only one reviews have been devoted to analysis of interactions of secondary structure is formed with two G4s, which G4 ligands of various chemical nature with their poly behave as independent quadruplex units. morphic nucleic acids targets, which is why we limited A multistep model is characteristic for unfolding of a ourselves to only recently published studies [208211]. G4 ensemble arranged as “beadsonastring” [111]. A wide repertoire of chemical approaches has been Furthermore, these multiquadruplex structures unfold at used for producing compounds with high affinity to G4s lower temperatures than individual G4s [193]. It was [208]. The synthetic G4 ligands include derivatives of shown in 2015 why the stability of the multiquadruplex anthraquinone (BSU1051), acridine (BRACO19,

BIOCHEMISTRY (Moscow) Vol. 81 No. 13 2016 GQUADRUPLEXES OF NUCLEIC ACIDS 1615 a Highest stability Intermediate stability 5′

Lowest stability 3′

b

3′ 5′

Similar stability of Gquadruplex units

Fig. 5. Model of multiquadruplex structure with G4 separated by threenucleotide linkers. a) Tandem Gquadruplexes formed by the

d((GGGTTA)11GGG) oligonucleotide in which the individual G4 display different thermodynamic stability due to different position of the flanking singlestranded regions (at 3′end, at both 5′ and 3′ends, at 5′end). b) In contrast, the oligonucleotide d(TTA

(GGGTTA)11GGGTTA) forms a structure in which each individual G4 neighboring trinucleotide fragment from both sides, thus reducing disparities in the stability of the G4 units. Residues T and A are highlighted by yellow and red circles, respectively.

AS1410, RHPS4), quinacridine (BOQ1, NCQ), por ity of interaction with G4 [223, 224], in particular with c phyrin (TMPyP4, NMM) [41], perylene (PIPER), tri ZG4 [225], induction of conformational transitions in azine (12459) [212], bisquinoline (360A, 307A) [213], the quadruplex target [226228], ability of inducing G4 and others. Furthermore, natural macrocyclic com formation (molecular chaperon functions), and high pounds capable of binding to G4 – telomestatin [214], selectivity of the G4–ligand interaction. The selectivity ligands based on natural alkaloids [58], such as berberine of smallmolecule compounds was often assessed by their [215], daunomycin [216], cryptolepine [217], HXDV, ability to interfere with biological processes associated pyridostatin [203, 218], and natural polyamines – have with G4 formation [210, 213, 229]. Attempts to evaluate been characterized. Actively investigated duplex DNA the selectivity of several commonly used G4 ligands by minor groovebinding ligands based on benzimidazoles monitoring the quadruplex melting using optimized exhibit ability to recognize G4s [219]. Even though some FRET techniques were reported [34]. Compounds that of the investigated ligands demonstrate high selectivity change their optical (luminescent) properties upon inter and affinity to G4, several of their properties do not allow action with G4 are of interest [207, 230233], as well as considering them as optimal. That is why in recent years reactive G4 ligands [234]. Smallmolecule compounds numerous compounds have been produced and investi exhibiting enhanced affinity to RNA quadruplexes [235 gated that in addition to the ability of binding to quadru 237] that stabilize or disrupt them during interaction plex structures provide such advantages as chemical sta [236] have been actively investigated in recent years. A bility and ease of synthesis, enhanced water solubility, series of new G4 ligands was discovered using molecular ability to penetrate into cells and low toxicity, recognition docking [122, 238]. The database (http://www. g4ldb.org) of G4 with particular topology [220222], chiral selectiv comprising a unique collection of more than 800 known

BIOCHEMISTRY (Moscow) Vol. 81 No. 13 2016 1616 DOLINNAYA et al. G4 ligands was created to facilitate the design of small nated nitrogen of the acridine ring can use the central molecules with predicted affinity to Gquadruplexes electronegative channel of the Gquadruplex to enhance [239]. interaction of the ligand with G4 structures. The possibil In most ligands, the G4recognizing site consists of a ity of structural adaptation of the quadruplex to the ligand planar polycyclic aromatic system that binds to the four was mentioned, for example reorganization of loops to stranded helix via interaction of πelectrons of aromatic increase the surface area of Gtetrads (to hexads and rings with the terminal Gtetrads. It was found recently octads) via incorporation of additional bases or base pairs that some G4 ligands were capable of discriminating of the loops into the plane of terminal tetrads. The Xray “upper” and “lower” tetrads of the same quadruplex crystallography data show that the type of G4 loops defin [240, 241]. However, G4s have other sites that demon ing the accessibility of quadruplex grooves significantly strate binding with small molecules: grooves with param affects the selectivity of the ligand [247]. eters varying for quadruplexes of different topology, phos It must be noted that all the intramolecular G4s phate groups, and loop bases. The ligands recognizing cocrystallized with smallmolecule ligands display paral these structural determinants can bind to G4 with a par lel topology [16, 215]. This is likely related with the dehy ticular secondary structure [242]. Narrow specificity of dration of the sample during crystallization (it is known such ligands is of great importance for their application as that dehydration induces formation of parallel G4) and novel therapeutic and diagnostic agents [214]. To impart constraints imposed by the crystal lattice. Interaction of the desired properties to small molecules, one can intro the ligand with Gquadruplexes of different conforma duce charged side chains and metal ions into them, and tions was also characterized using molecular dynamics the 3D structure of the ligand can be changed radically as simulation [248]. As of now, structures of approximately well [243]. 25 G4–ligand complexes have been deposited in the Most G4binding ligands stabilize the Gquadruplex Protein Data Bank (PDB) [248]. targets. G4 stabilization under the action of a low molec Despite the obvious desire to understand better the ular weight compound is determined by the balance of mechanism of molecular recognitions of G4 by aromatic electrostatic and stacking interactions, hydrogen bonds, ligands, only a few reports are available on investigation and hydrophobic and Van der Waals forces. The electro of thermodynamics of the complex formation. The ther static interactions are the most significant. Energy modynamic and structural characteristics of binding of parameters of G4 binding to ligands and methods for six different ligands with human telomeric DNA were their determination have been described [244]. Two pos compared in a paper in 2015 [226]. The analysis of exper sible mechanisms for G4 stabilization by ligands have imental data obtained from isothermal calorimetry, CD, been discussed: (i) decrease in the dissociation constant fluorescent spectroscopy, gel electrophoresis, and molec of the formed G4 structure, which results in increase in its ular modeling allowed estimation of dominating forces lifetime; (ii) increase in the G4 formation constant; in (specific interactions, changes in solvation and confor this case, the ligand initiates the quadruplex assembly. For mational state of the quadruplex) that controlled the example, the 360A ligand is capable of acceleration the binding of ligands to G4. Moreover, the existence of G4 formation 106fold. Several types of smallmolecule intermediate structures during G4 formation was taken ligands are known that cause destabilization or even dis into consideration for the first time. It was found that the ruption of quadruplex structures [245]. Some G4ligands parameters differed significantly for the poorly selective facilitate disturbance of functions, preventing and quadruplexspecific (highly selective) ligands. binding of the proteins of shelterin complex to telomeric Investigation of binding of aromatic ligands with DNA [66]. Ligands stabilizing G4s can inhibit their multimeric G4s showed that the ligand was usually incor unfolding by helicases competing with the proteins for porated between two G4 subunits forming a sandwich binding to G4 structures [213]. Small molecules are also like structure due to stacking interactions with terminal known to introduce damages into DNA, for example, Gtetrads of neighboring quadruplexes [249, 250]. pyridostatin causing double strand breaks [203]. Such Furthermore, the distance between the individual ligands are considered as effective antitumor agents quadruplexes in the multimeric system affected the effi because they affect cell viability, especially in the case, ciency of formation of these complexes [251]. However, it when the DNA repair system is inhibited or mutated was shown recently that one of the enantiomers of the [246]. chiral nickelcontaining ligand was not incorporated Structural information on ligand–G4 complexes has between the two quadruplex units, but rather covered been obtained using NMR spectroscopy [126] and Xray them from above, corresponding to two Gtetrads in size. crystallography [247]. It was stated in a review devoted to Furthermore, its binding with the Gquadruplex dimer structural analysis of such complexes [16] that the planar was 200fold more efficient than with the individual G4 aromatic site of the ligand did not intercalate into the [252]. quadruplex core upon its binding, but interacted with ter Metal complexes occupy a very important place minal Gtetrads. Positively charged groups such as proto among a huge number of organic molecules capable of

BIOCHEMISTRY (Moscow) Vol. 81 No. 13 2016 GQUADRUPLEXES OF NUCLEIC ACIDS 1617 binding to DNA quadruplexes, and they have been inves or introduce the quinone methide precursor into the tigated thoroughly in the last ten years. The G4ligands small molecule for its further chemical modification. based on metal complexes combine advantages of organ Considering, that the availability of bulky substituents ic compounds and coordinating action of a metal ion. could affect the transport of the ligand into the cell, as They are relatively easy to produce and exhibit unusual well as affinity and selectivity of their interaction with optical, magnetic, and catalytic properties, which makes G4, the strategy based on introduction of lowvolume them appealing for creation of libraries of the G4selec alkyne residues into the ligand seems more promising. tive ligands, Gquadruplex optical probes, and cleaving These groups can be transferred from the ligand to G4 agents. Exhaustive classification of binding of metal com via, for example, reaction between the nucleophilic group plexes to G4s (macrocyclic ligands, nonmacrocyclic in the quadruplex loop and an electrophilic center on the polydentate ligands, bulky metal assemblies with flat sur linker connecting the alkyne with the ligand [256]. Small faces, supramolecular chiral cylinders, luminescent metal molecules containing alkyne functions can be immobi complexes, and others) was presented in reviews [253, lized via the cycloaddition technique onto beads carrying 254] together with their structural peculiarities, addition azide groups, or they can be attached to fluorescent labels al geometric and electronic possibilities for the specific directly in the cell. Fluorogenic G4 ligands were used for binding to G4s, and mechanisms of their interactions optical visualization of Gquadruplex aptamers intro with DNA quadruplexes. Several types of metal complex duced into lung cancer cells [259]. The efficiency of cap es were designed to introduce damage and breaks into ture of Grich oligonucleotides was monitored by confo DNA. For example, a method for determination of strand cal microscopy, and the intracellular localization of the orientation in G4s using the reactive metal complex Zn quadruplexes thus formed was revealed. It was shown that TTAP based on phthalocyanine was developed [255]. parallel G4s were observed mostly in cell lysosomes, while This method is based on ligandinduced photocleavage of antiparallel structures were found in mitochondria. These the DNA strand between guanosines along the quadru findings are important from the point of view of drug plex axis, predominately after the guanosine belonging to delivery to specialized cell organelles using Gquadruplex the “upper” Gtetrad. aptamers. Alkylating G4 ligands are now considered as a class An innovative strategy for the synthesis of “smart” of chemotherapeutic agents [234]. Targeted DNA modi G4 ligands was developed recently based on template fication induced by these compounds can prevent correct mediated assembly of watersoluble compounds imitating translation of genetic information, causing death of Gtetrad (TemplateAssembled Synthetic GQuartet, tumor cells. In addition to medical application, the cova TASQ); moreover, this process occurs only in the pres lent modification of G4 using reactive ligands has been ence of a Gquadruplex target. For example, a novel mol suggested as an effective strategy for detection and moni ecule was designed and produced [260] with a structure toring of G4 formation in the entire genome and tran that could rearrange when it interacts with a G4, but not scriptome. Marking of G4sites can be performed via interacts with duplex DNA. The “smart” ligand forms affinity isolation of the respective DNA fragments with artificial Gtetrad via templatemediated intramolecular covalently bound highly specific ligands [256]. It is reaction, which binds to the terminal Gtetrad of the important for reactive molecules to minimize nonspecif quadruplex, stabilizing it in the process (Fig. 6). The ic nucleophilic attack and make the alkylation process metal (terbium) coordination in the G4 channel facili reversible, so that the DNA fragment isolated from the tates organization of the active closed state, and the pre genome would not carry covalently bound smallmole cisely located positive charges on the side substituents cule ligand on it. The electrophilic intermediate quinone enhance affinity of the ligand to G4 even further. methide was suggested as an alkylating agent attached to Application of these compounds as artificial receptors for the G4 ligand, which is capable of reversible alkylation testing the interaction of terminal Gtetrads in the and can form adducts with DNA that are stable in aque quadruplex with low molecular weight ligands was ous solutions [257]. The fact that quinone methide can be demonstrated [261]. The new generation of Gquadru easily produced from suitable watersoluble precursors plex biomimetic ligands is also capable of playing a role of via mild activation (photochemical, reductive, oxidative, “smart” fluorescent labels [262]. The ligand fluorescence thermal, and other) signifies its advantage [258]. Recently is quenched in the inactive open state due to intramolec developed chemical strategies for isolation and intracellu ular photoinduced electron transfer, while the fluores lar localization of Gquadruplexes based on modified G4 cence is restored in the closed state induced by the self ligands were summarized in a review [256]. The devel assembly of the artificial Gtetrad. The first such ligand – oped approaches allow a biotin residue to be introduced PyroTASQ based on pyrene – was shown to be an effec into a ligand, facilitating further affinity isolation of the tive G4specific probe for in vitro studies [262]. However, DNA quadruplex on streptavidincoated magnetic beads it showed a tendency for aggregation in intracellular [205], transfer a fluorophore from the ligand to G4 by medium. The specifically designed NTASQ with pyrene chemical reactions stimulated by shortdistance effects, replaced by a naphthalene residue was found to be suit

BIOCHEMISTRY (Moscow) Vol. 81 No. 13 2016 1618 DOLINNAYA et al. able for intracellular studies. NTASQ was used for the and their dissociation constants with RNA G4 (nanomo direct detection of RNA G4s in the nonpretreated (fixa lar range) were determined with the surface plasmon res tion, permeabilization, etc.) human and mouse cells onance technique. [263]. The proteins recognizing G4s belong to different Cellular and viral proteins. The availability of func classes and perform different functions in the cell: regula tionally important proteins capable of specific binding to tion of telomere length, ribosome assembly [272], tran G4 is one of most significant factors supporting the scription, translation, splicing, and alternative splicing hypothesis of biological relevance of these structures. [20, 269, 273276], DNA replication and reparation Most regulatory functions of G4s in cells are mediated by [277, 278], replicative bypass base damaged sites [279], the binding of proteins that modulate their thermody reverse transcription [206], conjugation of homologous namic stability and conformation. As of now, numerous chromosomes during meiosis, DNA duplex unwinding, proteins have been identified that specifically bind to changing DNA topology, and other processes of nucleic DNA quadruplexes [264266] and to the RNAanalogs of acid metabolism. The G4binding proteins are classified G4 [267, 268]. Affinity chromatography (for example, into three functional groups: (i) telomererelated pro using biotinylated G4forming oligonucleotides that are teins, such as proteins of shelterin complex [267, 280, linked to streptavidincoated beads) was applied for isola 281]; (ii) G4unwindig or cleaving enzymes, such as tion of target proteins followed by the massspectral DNA and RNAhelicases (molecular motors that analysis (LCMS/MS) [269, 270]. Identification and unwind structured nucleic acids and thus are involved in characterization of many cellular RNA G4binding pro numerous biological processes), nucleases [273, 282, teins (nuclear ribonucleoproteins, ribosomal proteins, 283]; (iii) proteins that stabilize Gquadruplexes and splicing factors) using developed screening system was prone their folding (molecular chaperons), for example, described in a recent paper [271]. The selected proteins nucleolin (multifunctional nuclear protein) and nucleo were characterized by MALDI TOF mass spectrometry, phosmin [269, 276, 284]. The proteins and enzymes with

a

b

Fig. 6. “Smart” G4 ligand capable of artificial Gtetrad formation via templatemediated intramolecular reaction; the terminal Gtetrad of G4 used as a template in the process. a) Chemical structure of the “smart” ligand, which rearranges itself into active (closed) state gen erating an artificial Gtetrad. b) Schematic representation of the mode of “smart” ligand action with G4binding domain of the molecule presented by a yellow circle and the guanine residues forming a new Gtetrad as pink rectangles.

BIOCHEMISTRY (Moscow) Vol. 81 No. 13 2016 GQUADRUPLEXES OF NUCLEIC ACIDS 1619 enhanced affinity to Gquadruplexes in comparison with peptide recognizes and binds predominately RNA double and singlestranded DNA not only discriminate quadruplexes due to the higher hydrophilicity of tyrosine such noncanonical structures, but can also recognize in comparison with phenylalanine. It was shown using their topology [269]. model structures containing modifications in the loops of Despite intensive investigation of protein–G4 com DNA and RNA quadruplexes (apurinic/apyrimidinic plexes, the molecular mechanisms for recognition of G sites, 2′Omethyl derivatives, or nucleosides with locked quadruplexes by protein molecules remain poorly under ribose ring (LNA, Locked Nucleic Acids)) that the Tyr stood, and investigations in this area are fragmentary and residues recognized primarily the ribose 2′hydroxyl unsystematic. It was established using highresolution groups. methods that protein–nucleic acid binding is affected by According to the modern paradigm, the G4s and the G4 loops [112] and duplex–Gquadruplex junction recognizing proteins are key players in many very impor [189, 285]. It was shown by molecular modeling that the tant metabolic processes. In particular, G4 structures are cavities in the HIV1 integrase and RecA protein considered as an endogenous source of chromosomal matched exactly the G4 size [55], and the domain of the instability [291] associated with numerous human dis nucleophosmin fit the G4 groove [286]. It was shown eases [292, 293]. Accumulated data indicate that if four recently using NMR spectroscopy that two peptide mole stranded noncanonical DNAs are not resolved by pro cules with sequences corresponding to prion protein frag teins, they can interfere with transcription and replication ments were bound to the terminal Gtetrads of RNA G4 processes [294, 295], as well as reparation and homolo via hydrophobic interactions (favorable change of water gous DNA recombination. This results in double strand entropy) [287]. An 18unit G4binding amino acid ed DNA breaks, genome rearrangements, and expansion sequence of RNAhelicase (RHAU) was identified in of Grich repeats [296298]. Moreover, genomic damages 2015 using the same method; it covered the end Gtetrad are greater the higher is thermodynamic stability of the of parallel DNA G4 and enveloped the quadruplex core G4 [139]. At the same time, it has been mentioned that due to electrostatic interactions between the three posi stable G4s are not the only reason for defective replica tively charged amino acids and the negativelycharged tion, and alternative mechanisms could exist that explain phosphate groups [288]. Interestingly, this binding model this phenomenon. For example, the DNA polymerase δ closely resembles one for most G4specific low molecular stalls near telomeric G4motifs independent of the weight ligands. Investigation of the crystal structure of a quadruplex structure formation on the lagging strand complex of arginine and glycinerich peptide fragment [299]; investigation at the cellular level showed that these of the FMRP protein with RNA containing Gquadru sequences were generally difficult to replicate. Unlike the plex and duplex domains with 2.8 Å resolution elucidated highfidelity replicative DNA polymerases, the special the molecular principles explaining the specificity of pro ized DNA polymerases from eukaryotic cells, which can tein–nucleic acid interactions and identified a wide net insert nucleosides opposite certain types of point dam work of contacts between the peptide and RNA, which ages, can prevent genomic instability in the vicinity of included not only the Gtetrad and boundary between the G4. Indirect indications exist that some of them, for G4 and the duplex domain, but were extended into the example Pol κ, Pol η, and Rev1 (members of Yfamily), RNA duplex domain [289]. It must be noted that FMRP can ensure efficient replication progress through DNA is a wellcharacterized regulatory RNAbinding protein quadruplexes [300]. The structural features of the most that plays a central role in the development of a series of investigated Rev1 explain why this polymerase operates human neurological disorders including autism. It was predominately on Grich templates. suggested that the interaction of this protein with RNA Helicases that prevent chromosomal instability quadruplexes directly affected regulation of translation of caused by G4forming sequences occupy a specific place hundreds of key mRNAs in neuronal cells, and the dis among the proteins specifically binding and unwinding ruption of these interactions was considered as one of the Gquadruplex structures [282, 298]. The mechanism and major mechanisms initiating pathological changes caus kinetics of G4 resolving by Pif1 family of replicases con ing mental disorders [20]. The role of aromatic amino served from bacteria to humans have been discussed in acids – tyrosine and phenylalanine – in the Cterminal [301303]. Interestingly, these helicases are activated in domain of proteins associated with liposarcoma and the process of G4 resolving and more readily unwind Ewing sarcoma in recognition of telomeric DNA and doublestranded DNA during replication. Unlike the RNA quadruplexes was investigated [290]. It was shown highly processive Pif1 family of replicases that remain that phenylalanine residues were extremely important for bound to their DNA substrate, G4resolvase 1 (also specific binding to G4. Thus, the replacement of three known as DHX36 or RHAU), which is capable of strong Phe by Ala residues prevented interaction of the peptide ly binding and resolving DNA G4 and RNA G4, is non with the Gquadruplex structure. Also, it was possible to processive, because it dissociates from the substrate after discriminate telomeric DNA G4s and RNA G4s by each act of ATP hydrolysis [304]. The unwinding of replacing the Phe residues with Tyr ones. This substituted intramolecular G4 by the ATPdependent DNAhelicase

BIOCHEMISTRY (Moscow) Vol. 81 No. 13 2016 1620 DOLINNAYA et al. BLM from the RecQ family is realized via different structures formed by LTRs promoter and silences HIV1 mechanisms depending of the Gquadruplex DNA sur viral transcription [276]. Moreover, it was established that rounding (single or doublestranded), as has been shown the Grich DNA sequence in the U3 region of the HIV1 by FRET [305]. The technique based on fluorescence virus that is capable of folding into G4 contains three bind methods allowed monitoring the unwinding of different ing sites of the Sp1 transcriptional factor, which is involved Gquadruplexes by DNAhelicases in real time [34]; G4 in regulation of the viral gene expression [100]. The G binding with smallmolecule quadruplexstabilizing lig quadruplex aptamers targeting HIV1 proteins that were and inhibited the enzyme activity, the inhibition degree considered as potential inhibitors of the viral gene replica depending on the G4 structure and the ligand type. tion in cells and viral integration in vitro [315] demonstrat Different efficiency of denaturation of G4s with different ed antiviral activity [316]. folding topologies by replication protein A (RPA) was G4specific antibodies. Gquadruplexes are immuno revealed by singlemolecule FRET [306]. G4 stabilizing genic like any other noncanonical DNA form. Anti factors, such as short loops (less than three nucleotide bodies are described in the literature that exhibit 1000 units) and more than three Gtetrad layers, helped to pre fold higher affinity to the fourstranded DNA in compar serve the Gquadruplex conformation even at the physio ison with duplex structures; furthermore, some of them logically relevant protein concentration, which increases are highly specific to parallel G4, while others bind either the functional significance of these structures [307]. to parallel or antiparallel Gquadruplex structures. The effect of Gquadruplexes on functioning of G4 Moreover, antibodies were isolated and characterized that binding proteins was investigated in several recent studies. display the ability to discriminate with 100fold specifici Thus, it was shown using single molecule technique that ty parallel G4s differing only in the structure of their telomeric DNA G4, which modulated telomerase activity loops [317]. Usually antibodies are produced from a huge in vitro, could affect the binding of other proteins involved library of bacteriophages, with each bacteriophage dis into telomere biology [118, 308]. And vice versa, proteins playing a unique antibody on its surface (phage display). binding to telomeric ends controlled DNA G4 formation in Bacteriophages carrying G4recognizing antibodies are the cell. Data are available on the effect of G4 on translo isolated via binding with immobilized DNA quadruplex cation of the telomerase catalytic subunit (TERT) from the es [317]. Antibodies of different specificity were success nucleus to mitochondria, which plays an important role in fully used as tools for quantitative detection of DNA and cellular apoptosis induced by the Gquadruplexbinding RNA quadruplexes in cells using different versions of ligands [309]. It was established that G4s of different topol immunofluorescence assay [318320]. ogy could inhibit topoisomerase Imediated nicking of Antibodies to Gquadruplexes were also used to doublestranded DNA [310, 311], thus affecting the degree demonstrate that fourstranded DNAs modulates gene of DNA supercoiling. The specialized lowfidelity DNA expression in vivo. The presence of such antibodies in polymerases hPol η and hPol ε from the Y and B families, human colon carcinoma cells caused significant changes respectively, which are capable of replicative bypassing in the expression of a large group of genes (from the basedamaged sites, retain various activity towards G4 investigated set consisting of more than 18,000 genes) containing substrates depending on the degree of specific whose regulatory regions are enriched with G4motifs binding with Gquadruplexes [279]. It was shown that in [321]. 20% of human genes G4 was a target for two components of the TFIIH transcriptional factor (XPD and XPB) [283]; furthermore, XPD acted as DNA G4helicase, and XPB as POLYMORPHISM OF TELOMERIC G4binding protein. Considering that both these compo GQUADRUPLEXES nents play a major role in coordinating the system of DNA damage identification and reparation mechanisms related Intramolecular Gquadruplexes formed by single to local melting of the double helix, it has been suggested stranded telomeric repeats in in vitro studies represent a that G4 can regulate these processes. A mechanism of G4 unique set of diverse topologies [148, 322]. The G4s mediated regulation of gene expression and other processes formed by human telomeric repeats are the best studied of DNA metabolism has been discussed [312]. This mech [57, 323], and this elevated interest is because they can anism is based on interaction of DNA G4s with yeast tran act as suppressors of tumor growth [66, 324]. scription coactivator Sub1 and its human homolog PC4. Telomeres are specialized nucleoprotein structures at In recent years, our understanding of the biological the ends of eukaryotic chromosomes, which protect the relevance of Gquadruplexes in prokaryotes [10, 98] and cells from chromosome fusions and DNA damage viruses [313] has increased. It was shown that G4s are responses. It is known that the telomeric DNA in somat specifically recognized by various viral proteins such as ic cells progressively shorten with each round of cell divi Epstein–Barr nuclear antigen I [103], coronavirus SARC sion due to inability of DNApolymerase to replicate the unique domain (SUD) existing exclusively in highly patho 3′end completely and due to nucleolytic processing. genic strains [314], and nucleolin, which stabilizes G4 After reaching a critical length (the Hayflick limit), the

BIOCHEMISTRY (Moscow) Vol. 81 No. 13 2016 GQUADRUPLEXES OF NUCLEIC ACIDS 1621 replication ceases and the cells enter a senescence phase ing nucleotide residues, DNA concentration [119], envi that precedes apoptosis. In contrast, a telomere length ronmental conditions such as ionic composition, avail maintenance mechanism is induced in tumor cells via ability of G4specific ligands [228], the degree of DNA activation of telomerase – an enzyme of ribonucleopro hydration controlled by PEG addition [328], on sample tein nature capable of synthesizing Grich repeats at the pretreatment, and methods of investigation [119]. 3′end of telomeric DNA according to the reversetran Moreover, it must be taken in consideration that the scription mechanism or via alternative lengthening of telomeric repeats form intermediate hairpin and G telomeres based on recombination (ALT). Increase in triplex structures in addition to the final G4 [299]. telomerase activity is observed in more than 85% of tumor It was shown that the topology of Gquadruplex cells, and the ALT mechanism is realized in 15% of formed by the d(AGGG(TTAGGG)3) oligonucleotide tumors. Since telomerase activity is either completely and by oligomers with similar base sequence differ signif absent or significantly lowered (as in stem and germ cells) icantly in the crystal state and in solution. According to in the absolute majority of cells in the organism, inhibi the Xray data, d(AGGG(TTAGGG)3) in the presence of tion of this enzyme would facilitate deceleration of tumor K+ folds into parallel intramolecular Gquadruplex with growth without toxic effects on the organism [325]. propellertype loops (PDB ID: 1KF1). At the same time, Folding of the singlestranded overhang at the chro antiparallel G4 and different variants of mixed (paral mosome ends into Gquadruplex structure can effective lel–antiparallel) forms of Gquadruplexes with various ly block the undesired extension of telomeric DNA via loop structures were identified in K+ solution [47]; fur preventing its hybridization with telomerase RNA, which thermore, the ratio between them was affected by the 3′ serves as a template for synthesis of telomeric sequences end nucleotides attached to the oligonucleotide. [326]. Quadruplex formation also prevents realization of However, the parallel intramolecular Gquadruplex, like the alternative lengthening of telomeres due to inhibition the one identified in the crystal state, was observed under of early recombination stages [18, 326]. It was shown that conditions of lower water activity (dehydration) caused the recombination proteins attached to DNA only after by addition of ethanol, DMSO, acetonitrile, or high unwinding of the telomeric Gquadruplexes by helicases. molecular weight PEG of different length [191, 329]. That is why stabilization of quadruplex structures in Because PEG was usually added to the oligonucleotide human telomeric DNA by a smallmolecule ligand is a solution to adjust the condition to intracellular molecular promising antitumor strategy [66]. The use of G4stabi crowding, until recently the intramolecular parallel struc lizing ligands can also cause telomere dysfunction inde ture of the G4 formed by the human telomeric repeats pendent of the telomeric DNA lengthening with telom was considered as a physiologically significant one [191, erase. For example, telomestatin can remove the telomere 329]. However, as shown recently, the presence of PEG shelterin protein TRF2, which results in damage of not so much imitates the high concentration of biopoly telomeric DNA in glioma stem cells and, consequently, mers as it facilitates dehydration of the sample, changing slowing the growth of glioblastoma – a malignant brain the water structure the same way as other cosolvents [18, tumor. It was found that the nonglioma cells were insen 330]. The PEGinitiated transition of the quadruplex sitive to the treatment with G4stabilizing ligand [327]. structure from the more compact mixed form into the Moreover, it was suggested that Gquadruplexes could be hydrodynamically less compact parallel one cannot be involved in capping and telomere protection from degra explained by the excluded volume effect, but rather can dation or end fusion. The Gquadruplex function as a be explained by the higher affinity of PEG to the parallel protective mechanism of chromosome ends, postulated G4 conformation, as shown in [331]. Moreover, the use of many decades ago, was clearly shown for yeast telomeres, other compounds instead of PEG more suitable for mim at least when all other forms of capping were defective icking the natural biological environment and creating [326]. high concentration of biopolymers such as 40% polysac The telomeric G4s are formed via intramolecular charide (Ficoll 70) or bovine serum albumin (300 mg/ml) folding of tandem Grich repeats, although it has been did not facilitate stabilization of the G4 parallel form mentioned in earlier studies that in some ciliates the [194, 332, 333]. The fact that it was precisely dehydration telomeric 3′overhangs form intermolecular Gquadru and not the excluded volume effect that induced forma plexes, which link together the macronuclear chromo tion of the parallel quadruplex was shown in 2013 [164]. somes. In that study, the structural and mechanical properties of The use of Gquadruplexes of telomeric DNA as tar human telomeric quadruplex were investigated at the sin gets of antitumor reagents requires knowledge of the gle molecule level using optical tweezers. detailed G4 structure under conditions mimicking intra Either increase in the cosolvent amount or high cellular ones. The issue is complicated by the fact that the DNA concentration (69 mM) can cause conversion of structure and stability of the most investigated Gquadru antiparallel G4 into the parallel one [334]. The oligonu plexes formed by the four human telomeric DNA repeats, cleotide itself can play a role of the agent mimicking d(TTAGGG), strongly depend on the presence of flank molecular crowding in such concentrated solutions.

BIOCHEMISTRY (Moscow) Vol. 81 No. 13 2016 1622 DOLINNAYA et al. Despite differences in the action mechanism, both these revealed that the conformation of the quadruplex units in factors result in the dehydration effect, that is decrease in the long strand was different from the conformation of the water activity [335]. The concentration dependence of isolated G4. The end and inner quadruplexes exist pre the G4 topology can provide an explanation why different dominantly as a twotetrad antiparallel “basket” and a experimental methods, which require DNA samples with structure with mixed topology with three Gtetrad layers concentrations differing by orders of magnitude, reveal arranged as “beadsonastring” [194]. The unusual two different types of quadruplex folding for the same tetrad antiparallel G4 binding only one cation in the oligonucleotide. It is of interest that G4 stabilized with quadruplex cavity was documented with a combination of sodium ions maintains antiparallel topology independent physicochemical methods at extremely low concentration of the DNA concentration [119]. of potassium or strontium ions [22]. It is commonly accepted that the structural polymor The proof that telomeres fold into Gquadruplexes phism of telomeric repeats is much less pronounced in of various types under in vivo conditions allows new com solution containing Na+ than in K+ solution. For exam prehension of the data according to which not all G4 + ple, the d(AGGG(TTAGGG)3) oligonucleotide in Na conformations actively inhibit telomere lengthening by solution forms exclusively the antiparallel threetetrad telomerase, including human telomerase [18]. In particu G4 with “basket”type conformation. However, forma lar, parallel tetramolecular G4s are good substrates of the tion of the antiparallel intramolecular structure differing enzyme from Tetrahymena; the parallel intramolecular from the standard quadruplex by the nature of hydrogen quadruplexes are also lengthened by telomerase. At the bonds in Gtetrads and by the loop locations was shown same time, the intramolecular antiparallel quadruplexes recently by NMR spectroscopy for longer oligomers con (that is the ones that have been postulated) are resistant to taining nucleotide units flanking the G4 core [127]. lengthening under the action of telomerase [194]. These Different conformations of Gquadruplexes formed by are precisely the G4 formed by the singlestranded telom telomeric sequences and their dynamics in Na+ solutions ere ends that are capable of inhibiting telomerase acting was investigated using singlemolecule FRET [336]. This as tumor suppressors. method allows characterization of nucleic acids structur Structure and stability of Gquadruplexes in elongat al polymorphism and the kinetics of conformational tran ed telomeric DNA. In the last decade, conflicting reports sitions on a time scale from milliseconds to minutes. In have been published on the structural arrangement and addition to the unfolded state, at least three different stability of Gquadruplexes in such DNA in vitro. Data of telomeric quadruplexes were identified under dynamic CD spectroscopy and of electrophoretic studies indicate equilibrium. These data change our perspective on the that the long telomeric sequences predominantly fold into limited conformational options of telomeric G4s in Na+ intramolecular rather than intermolecular quadruplexes. solutions and indicate the polymorphic nature of the Experimental confirmations were obtained for both the telomeric repeats under these conditions (see reviews on “beadsona string” model in which the individual G4s telomere structure in [57, 281]). In a study published in were independent [194], and for the model in which the 2016, conformational potential of telomeric DNA was contiguously stacked Gquadruplex units affected each investigated under conditions of low cation concentra other [111, 193, 337]. The results of optical tweezers tion, and it was shown that the conversion of the antipar investigation demonstrated that only 5% of higher order allel G4 into the parallel one occurred when a minor G4 structures were formed by the DNA fragment con amount of KCl was added to the Na+ solution [22]. taining 24 d(TTTAGGG) repeats, the length comparable Taking into consideration the fact that the level of K+ with the total singlestranded human telomeric overhang, in mammalian cells (approximately 100150 mM) is sig while the clear majority of the quadruplexes behaved as nificantly higher than the content of Na+, the G4 structure “beadsonastring” [162]. The contradictions related to formed in the presence of K+ seems more relevant physio the arrangement of multiquadruplex telomeric systems logically. The conformation of d(AGGG(TTAGGG)3 in were partially explained in a work published in 2016 [31]. live X. laevis oocytes and ex vivo in cellular extract of these It was found that realization of one model or another oocytes where the natural conditions of molecular crow depended on the ionic composition of the medium. The ing were realized was investigated in 2013 [194]. It must be individual G4s practically do not affect each other in the noted that the recently developed incell NMR technique K+ solutions, while Na+ facilitated interaction of quadru was used for in vivo studies, which allowed evaluating of plex subunits. These are precisely the interactions that the nucleic acids structure in the eukaryotic intracellular make the quadruplex structure formed by the environment. It was shown using this approach and using d((GGGTAA)7GGG) oligonucleotide more stable in the + fluorescence spectroscopy that d(AGGG(TTAGGG)3) Na containing solutions than in the presence of KCl. adapted the Gquadruplex structure with mixed topology There is some disagreement in the published data on (3 + 1). The same structure is formed in diluted K+ solu the number of formed G4 units in the long telomeric tion (but not in the presence of Na+). Investigation of a sequences. Thermodynamic studies revealed that more fragment of telomeric DNA containing 8 and 12 Gtracts than 90% of the oligonucleotides d(TTAGGG)12 and

BIOCHEMISTRY (Moscow) Vol. 81 No. 13 2016 GQUADRUPLEXES OF NUCLEIC ACIDS 1623 d((TTAGGG)12TT) fold into three adjacent Gquadru ing on localization of the oxidized base. It must be men plexes, in other words into the structure with the maximum tioned that the reparation of natural damages in telomer possible numbers of G4s, and only 10% form the two ic Gquadruplexes remains poorly understood. quadruplex structure [111]. Nevertheless, it has been men tioned that in the case of very long telomeric repeats (∼200 nucleotide residues), formation of the maximum amount GQUADRUPLEXES FORMED IN PROMOTER of G4s becomes energetically unfavorable [111]. The direct REGIONS OF EUKARYOTIC GENES visualization of the d(TTAGGG)16 telomeric repeats with singlemolecule atomic force microscopy [197] supported It was shown using bioinformatics approaches that the “beadsonastring” model, where the G4 were sepa more than 40% of genes encoding human proteins con rated by singlestranded DNA regions, which in turn cre tained at least one G4motif in a promoter region. The ated more flexible structure with the number of quadru Gmotifs located in the promoters of human oncogenes plexes not at the maximum level possible. Such only partial and the genes of proteins expressed in tumor cells or folding of the long telomeric DNA provides the possibility involved in tumor angiogenesis, unlimited replication, of binding of the telomere protective protein POT1 with deregulation of apoptosis, and metastasizing are the most singlestranded sites. In addition to the proteins of shel popular study objects: cMyc [113, 138, 140, 157], Bcl2 terin complex, a whole series of telomere processing [87], cKit1, cKit2 [142, 347, 348], cMyb, WT1 [349], enzymes requires free 3′end for binding and further func VEGF [114, 350], VEGFR2 [351], RET [352], Rb, HIF tioning. The minimal size of the singlestranded binding 1α, KRAS, PDGFA [353], and PDGFRβ [354], tran site (612 nucleotides) for these enzymes was determined scription factors Nrf2 [227], SRC [203], as well as the pro in in vitro experiments [338]. Considering that Gquadru moter of HIV1 genes [99, 355], 3′proximal promoter plexes are formed more readily at the 3′end of DNA region of the human tyrosine hydroxylase gene (TH) [197], and that the probability of folding into quadruplex associated with neurological disorders [356], promoter of structures decreases on moving towards the 5′end of the the human telomerase reverse transcriptase gene telomeric DNA (from 55% to 21.8, 14.5, and 7.9% for the (hTERT) [357, 358]. Under certain conditions, the mini 1st, 2nd, 3rd, and 4th G4 position, respectively), the length satellite repeats from the ILPR, which is localized 363 bp of the singlestranded 3′end region can vary from 0 to 18 upstream from the insulin encoding sequence, can also be nucleotides (three d(TTAGGG) repeats) in the case of assigned to this category [359]. human telomeric DNA [197]. It was noted that the size of Oligonucleotides containing four consecutive G singlestranded site as a result of coordinated action of G4 tracts, sometimes with flanking regions, were usually used formation and its unwinding by helicases affected telomere for in vitro investigations of the secondary structures lengthening by telomerase or DNA polymerase (ALT formed by G4motifs from gene promoters [45]. As mechanism) [338]. shown using NMR and CD spectroscopy and by chemi Gquadruplexes with modified nucleotide residues. cal probing, these oligonucleotide models usually folded The effect of guanine analogs (2aminopurine, 8bromo in K+ solutions into parallel intramolecular quadruplexes and 8methyl guanine, hypoxanthine, and others), sub [8, 227, 350], although conformational heterogeneity of stituted or modified ribose residues (LNA), and modified the promoter G4s was reported in some publications. The nonguanine bases in the G4motif on the folding topol common features of the parallel G4s dominating in the ogy and stability of intra and intermolecular Gquadru population include three Gtetrads connected by two sin plexes [339341], as well as on the functioning of proteins glenucleotide loops (first and third) and the middle loop recognizing G4 structures [342] was explored in several variable in length [323, 350, 360]. For example, loops 1 : recent works and reviews. It was mentioned that certain 2 : 1 are characteristic for the cMyc quadruplex, and for types of DNA damages could act as modulators of G4 the G4 VEGF – 1 : 4 : 1 [350]. Despite the indicated com formation. The effect of natural modifications of bases mon features of promoter quadruplexes, it has been sug (oxidative damages, apurinic sites, alkylated derivatives, gested that each G4 can assume a unique structure due to and others) localized either in the loops or in the quadru interaction of the nucleotides from the middle loop with plex core of human telomeric Gquadruplexes has been flanking sequences [350]. Conformation of G4s from the discussed in detail [343345]. As a rule, the analogs of gene promoter regions was also investigated by Xray bases that replace guanines in the Gtetrad significantly crystallography [361]. It was established that a dichotomy destabilize G4. The loop modifications change the struc between the structure in crystal state and in solution, ture of the quadruplex and its stability less dramatically, which was characteristic for telomeric quadruplexes, was and the effect depends on the type of damage and its loca not extended to the other eukaryotic Gquadruplexes. tion in the base sequence. For example, apurinic sites in Considering that many Gmotifs in promoter loops of DNA G4 facilitate formation of propeller loops regions contain more than four Gtracts, they can form and stabilize the parallel Gquadruplexes [346]. And 8 several discrete quadruplexes depending on what combi oxoA either slightly destabilizes or stabilizes G4 depend nation of Gtracts is used for in vitro studies, its length,

BIOCHEMISTRY (Moscow) Vol. 81 No. 13 2016 1624 DOLINNAYA et al. and availability or absence of flanking regions. The vari (iii) tandem of two G4s interacting with each other, (iv) ous G4 conformations can be at dynamic equilibrium multiple G4s formed by overlapping G4motifs. Evidence with each other [138, 350]. The set of quadruplex con of the interactions between quadruplexes formed by formers formed in the cMyc promoter as well as the sequences from promoter regions with multiple Gtracts effect of loops and flanking nucleotides on thermody has been presented in several reports [358, 365]. namic stability and kinetics of the G4 folding was evalu Formation of G4 multimers can be a characteristic fea ated [138]. The dependence of the results on the selected ture of the promoter G4s, because it is exactly the paral sequence can be clearly illustrated using the promoter lel G4s that demonstrate a tendency for “sticking” to region P1 of the Bcl2 gene as an example. The 39nt G each other. The interaction between two individual G rich sequence (Pu39) contains six Gtracts from 35 con quadruplexes formed by the promoter region of the secutive guanosine residues. Investigation of the confor hTERT gene containing 12 Gtracts was investigated in mational potential of the set of oligonucleotides (shorter most detail (Fig. 7a). It must be mentioned that contro than Pu39) with partly overlapping sequences containing versial opinions have been expressed in the published data four consecutive Gtracts showed that they could form on the number of G4s formed by this sequence. On one various quadruplex structures, which could bind G4spe hand, arguments have been presented in favor of the exis cific ligands with different degree of selectivity [362, 363]. tence of three parallel G4s interacting with each other via Moreover, these Gquadruplexes were not parallel but stacking interactions of the end Gtetrads [358]. On the had mixed topology (3 + 1), which excluded them from other hand, the formation of a twoquadruplex structure the common trend. The MidG4 formed by four central has been reported, in which the components formed a Gtracts was the most stable. However, when the full unified structure; the formation of parallel G4 with four sized Pu39 was used as a model, the prevailing structure consecutive Gtracts (IIV) and formation of a quadru into which it folded comprised an intramolecular parallel plex with unusual conformation formed by two pairs of quadruplex with two singlenucleotide loops and a middle consecutive Gtracts (V, VI and XI, XII) separated by 13nt loop. The Gtracts I, II, IV, and V participated in 26nt loop (tracts VIIX) was shown by CD spectroscopy, formation of this quadruplex, as shown by chemical foot Taqpolymerase inhibition, chemical footprinting, and printing and NMR spectroscopy, and the guanosine optical tweezers methods (Fig. 7b). This loop likely forms residues of Gtract III were included in the middle loop a stable hairpin, which can explain high stability of this [87]. Moreover, the fullsized parallel G4 was found to be atypical Gquadruplex [195]. Direct evidence of interac even more thermodynamically stable than MidG4. The tion between two G4s obtained with optical tweezers was presence of several topologically different quadruplexes reported in 2016 [195]. This approach was modified in in the same regulatory region can be important for fine such a way to break down the entire structure into indi tuning of gene expression mediated by the binding of dif vidual components and to monitor sequentially the ferent G4s with different proteins. According to recent dynamics of conformational transitions in each G4com data, in the close vicinity of the P1 promoter of the Bcl2 ponent without disrupting contacts between the G gene there is another 28nt G4forming sequence P1G4, quadruplexes. To target the desired domain of the bio which can fold under physiological conditions into two molecule, the reaction of alkyneazide cycloaddition to parallel G4s that are in a state of equilibrium with each the alkyne group attached between two analyzed G4s and other. It was shown using chemical footprinting and 3′ and 5′ends of the construct was used. This allowed NMRspectroscopy that one of the quadruplexes con targeted addition of dsDNA handles with a terminal azide tained two singlenucleotide loops and 12nt middle group and separate monitoring mechanical folding– loop, while the other had unusual conformation with unfolding of one of the Gquadruplex components, leav three singlenucleotide loops and 11nt site protruding ing the other part of the biomolecule free of stress from the G4 core [364]. The long loops in both quadru (Fig. 7c). It was the authors’ opinion that this approach plexes assume the hairpin duplex conformation, which provided a significant advantage over the use of truncated differentiates them from other parallel G4s and can be mutants, in which a part of the structure is deleted. The specifically recognized by small molecules. The authors developed technique for the analysis of high order G suggested that the presence of Pu39 and P1G4 in the quadruplex structures provided the possibility to deter neighboring regions of the P1 promoter provides an addi mine hierarchy of the unfolding of the analyzed system tional mechanism for regulation of the Bcl2 gene tran (the less stable G4 at the 5′end of the molecule unfolded scription. Furthermore, the P1G4 sequence plays a criti first, followed by the more stable 3′end G4 with the cal role in the repression of transcriptional activity [364]. structured middle loop), and it was possible to estimate The occurrence of various G4s formed in gene pro the stabilization energy of π–π interactions between the moters was discussed in a review published in 2010 [70], terminal Gtetrads in the interquadruplex interface and their classification was presented. Four classes of (2 kcal/mol) [195]. It should be noted that the G4multi intramolecular quadruplexes were suggested: (i) single mers in this work are considered as elements of the terti G4, (ii) pair of different G4 separated by ∼30 base pairs, ary structure, which is uncharacteristic for genomic DNA

BIOCHEMISTRY (Moscow) Vol. 81 No. 13 2016 GQUADRUPLEXES OF NUCLEIC ACIDS 1625 unlike in proteins and RNA molecules. Usually conclu plex. It was shown in earlier studies that oligonucleotides of sions on the spatial organization of multiplex G4 are various lengths from the promoter region of the KRAS gene based on knowledge of the structure of quadruplex units in KCl solution folded into G4s of different topology, in its composition. It was shown in a study devoted to including monomeric forms [367]. direct evidence of interaction between two G4s formed by Effect of promoter G4 on gene expression. Plasmid the human ILPR sequence (d(ACAGGGGT constructs with inserted Grich promoter regions or their

GTGGGG)4) [359] that this principle was not obeyed. fragments are better for mimicking in vivo conditions. The data were obtained by chemical footprinting and Unlike in the singlestranded telomeric ends, the forma optical tweezers techniques indicating that the conforma tion of Gquadruplex structure in the promoter regions tion adapted by the intramolecular quadruplexes could occurs in competition with preservation of the double not be automatically predicted based on the structure of helix and is regulated by the level of DNA supercoiling individual G4, and the characterized interquadruplex and binding with G4recognizing proteins. The G4 for interactions differed from those observed in telomeric mation could be energetically favorable only in negative sequences. The availability of “tertiary” interactions ly supercoiled genome fragments (or plasmids imitating between the neighboring G4s can produce an important them) [113]. The mechanism of regulation of cMyc gene biological impact. The extended rigid quadruplex struc transcription has been elucidated using plasmid models in tures can cause more serious errors in the replication a conceptual study [113] where the major role was processes, create new targets for G4specific ligands and assigned to Gquadruplexes. Participation of G4 struc cellular proteins, and ensure finetuning of the gene tures formed in promoter regions in inhibition of onco expression level. gene expression has been postulated in many recent pub It is generally accepted that tandemarranged G lications. That is why the use of low molecular weight lig tracts composed of three or more consecutive guanosine ands, which specifically bind and stabilize G4s, is a basis residues participate in the formation of intramolecular G4 for antitumor strategy [8, 229]. forming “edges” of the quadruplex core, while the linker A strong effect of the G4 location in the eukaryotic sequences connecting Gtracts become the quadruplex gene promoter on the level of transcription was shown in loops. However, an exception from this rule was found recent publications using reporter constructs [368]. recently using NMR spectroscopy and Xray analysis. The Whereas the Gmotif in the antisense (template) strand sequences of Pu24 and cKit87 from the human promoters inhibits transcription significantly, its localization in the cMyc and cKit [361], respectively, can fold into unusual sense (coding) strand does not affect the efficiency of the G4s. The characteristic feature of such quadruplexes is that process. More complicated regularities related to the the guanosine tract in one of the “edges” is interrupted, position effect of Gmotifs in regulatory sites were despite the presence of four full Gtracts. For example, the revealed during investigation of the role of G4s in the structure formed by cKit87 investigated in vitro exhibits expression of bacterial genes [369]. It was established that unique topology like none of the known G4s. Despite the the degree of transcription inhibition in the case of G4 availability of four (GGG) tracts in the cKit87 sequence location in the antisense chain of the promoter site corre

(d(A1G2G3G4A5G6G7G8C9G10C11T12G13G14G15A16G17G18 lated with the G4 stability. However, when the G4motif A19G20G21G22)), which suggests formation of the standard was introduced into the antisense strand between the TSS parallel G4, the separately positioned residue G10 partici and stop codon, an increase in the level of gene expres pates in formation of one of the “edges” of the experimen sion was observed. As suggested by the authors, the G4 tally detected quadruplex together with only two of the formed beyond the promoter facilitated double helix three guanosines (G21 and G22) at the 3′end of the mole unwinding, thus supporting the unwinding activity of cule. The unusual quadruplex structures formed by the RNA polymerase. Enhancement of promoter activity was

32nt oligonucleotide d(G1C2G3G4T5G6T7G8G9G10A11A12 also observed in the case when Grich sequence with G13A14G15G16G17A18A19G20A21G22G23G24G25G26A27G28G29 seven Gtracts was located at the 3′proximate region of C30A31G32) from the KRAS gene promoter were recorded the human TH gene promoter [356]. It was suggested that using NMR spectroscopy, CD, and other methods [366]. one of the reasons for promoter activation was the forma This oligomer folds in K+ solution into two dimeric tion of multiple quadruplexes by these G4motifs, which quadruplexes at the 5′ and 3′ends of the molecule, while could differentially regulate the gene expression. the central segment A11A21 only connects two quadruplex Because gene expression is insensitive to the avail units even though it is enriched with G residues. One of the ability of G4s in the sense strand of the promoter region characteristic features of these structures is the fact that the [368], it follows that the quadruplex structure in the C

C2 residue that disrupts the Gtract at the 5′end bulges rich antisense strand (imotif) of the promoter region from the Gquadruplex core. The described dimeric G4s either does not form intracellularly or does not affect the cannot be formed in the genome context; however, it is the transcription process. However, participation of the i authors’ opinion that conditions of molecular crowding motif in transcription regulation was not ruled out in can facilitate the intramolecular assembly of the quadru other publications. For example, it was shown using the

BIOCHEMISTRY (Moscow) Vol. 81 No. 13 2016 1626 DOLINNAYA et al. methods of molecular population dynamics and optical RNA G4s under different conditions in vitro and in fixed tweezers that the small molecules and proteins interacting and live cells based on the use of the fluorogenic cyanine with imotif target could modulate transcription of the dye has been developed [377]. Bcl2 oncogene [370]. It was suggested that while the G4 Telomeres – the specialized DNA–protein struc could act as an inhibition signal for the oncogene expres tures at the ends of eukaryotic chromosomes – for a long sion, the imotif could activate this process [184]. time were considered transcriptionally inactive. However, Correlation between point mutations in G4motifs recent studies have shown that telomeric DNA were tran that affected conformation and stability of quadruplexes scribed in mammalian cells with formation of long non and variation in the gene expression profiles of humans coding RNA (TERRA) that contain repeats of the 5′ was analyzed [371]. In addition to the development of UUAGGG3′ sequence. These G4motifs exist as areas affiliated with personalized medicine, these findings quadruplexes in K+ solutions and in vivo [1, 57, 81, 378]. have been related to evolutionary aspects. It was implied The fact that the human TERRA can fold into stable G that the elements of the quadruplex core remained evolu quadruplex structures was demonstrated using CD and tionarily conserved, while loops in G4s were subjected to NMR spectroscopy, Xray crystallography, and mass mutations. spectrometry [1, 125, 379]. The formation of parallel G4 from human TERRA molecules in live cells was demon strated using oligonucleotide probes with lightswitchable STRUCTURAL FEATURES pyrene groups [1]. Series of oligonucleotides were synthe OF RNA QUADRUPLEXES sized for this purpose that contained the 5′GGGU AND THEIR BIOLOGICAL RELEVANCE UAGGG sequence with two Gtracts and with pyrene residues attached to their ends via flexible linkers. The The same as the DNA sequences, RNA analogs con two pyrene molecules were spatially separated in the taining Gtracts are capable of folding into quadruplex unstructured state, and their fluorescence signal was weak structures under physiological conditions, with stabiliza (monomeric emission). However, the pyrene molecules at tion factors and folding pathways similar to those the 5′ and 3′ends of the oligonucleotide probes were observed for DNA quadruplexes [372]. As in the case of brought together during the formation of the bimolecular DNA G4s, the length and base sequence of the loops, parallel G4 in the presence of K+, forming the fluores concentration of K+ and Na+, and number of Gtetrads cenceexcited excimer state (Fig. 8). The change in color are the major factors of RNA quadruplex stability [96, of the excimer fluorescence observed by fluorescence 373]. Considering that molecules of ribonucleic acid are microscopy allowed real time monitoring of G4 forma usually singlestranded, RNA G4 formation should occur tion in HeLa cells incubated with oligonucleotide probes. more easily than in the case of doublestranded DNA, Unlike the polymorphic DNA quadruplexes, the because hybridization with the complementary sequence RNA G4 adopt only parallel topology [57, 380]; more will not compete with the process of quadruplex assembly. over, this is also true for both short oligonucleotide mod However, it has been mentioned that the nucleotide con els [57, 81, 380] and long telomeric RNA forming a gar text is one of the major factors controlling the G4 folding land of intramolecular quadruplex structures [192]. It was in RNA molecules. Thus, the availability of Ctracts in shown that parallel orientation of Gtracts in the quadru the vicinity that are capable of hybridization with the G4 plexes formed by TERRA RNA did not depend on the motifs interferes with the formation of fourstranded base sequence of loops, nature of monovalent cations (K+ RNA structures [95]. or Na+), state of the sample (crystalline or in aqueous Many G4motifs have been identified in the human buffer), and the presence of smallmolecule ligands [379, transcriptome. According to data of bioinformatic analy 381]. It is known that all guanosines in the G4 of parallel sis, they are present in the 5′UTR of more than 2000 topology have anticonformation, while in the antiparal human genes [374], as well as in 3′untranslated sites lel G4, half of the residues have anti and another half – [375]. The G4motifs were found in various regions of synconformation. That is why the conformational pref mRNA encoding or not encoding proteins, for example, erences of nucleosides (synanti) can define the mutual in the open reading frame of certain mRNA [376], in sites arrangement of strands in the Gquadruplex. Since rG of alternative processing of premRNA, as well as in pre residues in oligo and polyribonucleotides are predomi microRNA [82], in long noncoding RNA [83], and in nantly in anticonformation due to the steric hindrance viral RNA. A new approach for detection and mapping of imposed by the 2′hydroxyl group, and the dG readily RNA G4s in cellular transcripts has been described [206]. assume the synconformation also, the parallel topology It is based on the monitoring of the reverse transcriptase is characteristic for Gquadruplexes with ribonucleotide stops due to formation of RNA G4; it has been shown residues. Transition of the antiparallel G4 formed by the that this process correlated with the stability of RNA aptamer to thrombin (5′d(GGTTGGTGTGGTTGG)) quadruplexes, which was controlled by metal ions and to the quadruplex with parallel topology was achieved via G4specific ligands. A promising strategy for detection of partial or complete replacement of the dG residues by rG.

BIOCHEMISTRY (Moscow) Vol. 81 No. 13 2016 GQUADRUPLEXES OF NUCLEIC ACIDS 1627 a

b

c

Fig. 7. Evaluation of the energy of interaction between two quadruplexes formed by the promoter region of the hTERT gene containing 12 G tracts (a) using optical tweezers (b). The reaction of alkyneazide cycloaddition was used for mechanical unfolding–assembly of the target domain of the biomolecule; the alkyne group placed between two analyzed G4 allowed targeted addition of the dsDNA handles containing the azide group. Stretching–relaxation of different combinations of dsDNA handles (indicated by green arrows) immobilized on optically trapped beads to monitor the dynamics of conformational transitions and their energy in the Gquadruplex tandem and in each G4compo nent separately (c). Laser beams focused onto the beads are presented as yellow cones.

Moreover, this replacement resulted in conversion of the monomolecular G4 into a bimolecular one due to incom patibility of the loop lengths of the quadruplex with the parallel intramolecular folding of the riboversion of the aptamer [382]. The RNA quadruplexes are usually more stable than the G4s formed by the same DNA sequence [380]. For example, Tm and ΔG (at 310 K) of the RNA quadruplex containing three Gtetrads and singlenucleotide loops in solution with 15 mM concentration of cations are 359 K and 9 kcal/mol, respectively, versus 350 K and 5 kcal/mol for the DNA analog [131]. More likely, the difference in the properties of two nucleic acids is the reason for that, rather than the difference in the folding topology of the Fig. 8. Use of 5′GGGUUAGGG oligonucleotides with two G quadruplexes [57, 380, 383]. The availability of the 2′ tracts containing pyrene residues at the 5′ and 3′ends for demon OHgroup plays a significant role in organization of the strating formation of parallel bimolecular RNA G4. In the unstructured state, the pyrene fluorescence signal is weak hydration shell in the grooves of the fourstranded struc (monomeric emission). The pyrene residues are brought together ture, in formation of the network of hydrogen bonds, and during complex formation, forming fluorescenceexcited excimer in conformation of the sugar residues. According to the state (shown with green ovals).

BIOCHEMISTRY (Moscow) Vol. 81 No. 13 2016 1628 DOLINNAYA et al. molecular modeling data, the additional Hbonds formed the suppression effect and increase the level of translation with participation of the 2′OHgroup and electron of this mRNA in eukaryotic cells [236]. The reaction of acceptor centers such as oxygen atoms of the sugarphos alkyneazide cycloaddition in situ was used for identifica phate backbone (O3′, O4′, O5′) and polar exocyclic tion of ligands selectively binding to the TERRA G4 but groups of the bases (NH2group) provide significant con not to the telomeric DNA quadruplex [235]. tribution to stabilization of Gquadruplexes of parallel Conformational transitions from duplex to G topology [381]. Crystallographic studies showed that the quadruplex mediated by metal ions, by oligodeoxyri sugar residues in the guanosines from the end tetrads had bonucleotides of certain primary structure, by proteins, C2′endoconformation, while the C3′endoconforma and by other agents represent a moving force for switch tion was characteristic for the guanosines in the center of ing the activity of the specially designed ribozymes and the quadruplex core, which was significantly different DNAzymes [389391]. from the corresponding parameters of the DNA quadru Parallel RNA quadruplexes exhibit a strong tendency plex [381]. These findings agree with the data of NMR to stick together [379, 381]. For example, the oligonu spectroscopy and computer modeling [381]. As in the cleotide with two telomeric repeats r(UAGGGU case of DNA G4s, thermodynamic stability of RNA UAGGGU) form in K+ or Na+ solutions bimolecular par quadruplexes decreases with increasing loop lengths [96]; allel quadruplexes that dimerize via stacking interactions furthermore, on one hand this effect is more pronounced, of the 5′end Gtetrads. The lack of UA residues at the 5′ and on the other it is governed by more complex regular end of the molecule facilitates formation of dimeric RNA ities than in the case of DNA quadruplexes [96, 384]. The quadruplexes even more. Moreover, as shown by NMR effects of the number of nucleotide residues in loops, spectroscopy, two additional adenine residues from UUA length of Gtracts, and potassium ion concentration on loops were brought into the plane of the end Gtetrads, the thermodynamic stability of RNA quadruplexes and thus increasing the surface area of the stacking contact the degree of cooperativity of their folding have been [81]. It has been suggested that the hexad A·(G·G·G·G)·A characterized [96, 373]; the G4 topology remained is stabilized by Hbonds between N1 of adenine and 2′ invariably parallel. It was shown on the example of the OH of guanosine [379]. Dimerization of parallel RNA r(GGGGCC)n sequence from the C9orf72 gene transcript quadruplexes via stacking interactions of G·(A)·G·G·(A)·G that depending on the RNA concentration, length of hexads was also reported for the G4 formed by the repeats, and availability of flanking sequences, this type of r(GGAGGAGGAGGA) oligonucleotide in the presence oligonucleotides could form either very stable parallel of potassium ions. The propensity of RNA G4 to multi intramolecular quadruplexes with propellertype loops, merization is an important factor inducing formation of or parallel tetramolecular RNA G4 [385]. A mechanism the highorder structures in long RNA sequences [192]. was suggested recently according to which G4 formation According to massspectral analysis, the TERRA forms in the long (GGGGCC) repeat both on the level of DNA stable multimeric G4. It was suggested that they could be and RNA initiates a molecular cascade of neurodegener arranged as “beadsonastring” in which each bead com ative disorders [292]. prised either a single RNA G4 or a pair of quadruplexes Some sufficiently long RNA molecules can form combined via stacking interactions [192]. These RNA several stable intramolecular conformations that coexist quadruplex dimers could serve as targets for ligands recog with each other [386]. For example, the double helical nizing the Gtetrad planes by intercalating between them hairpin structure can compete with formation of RNA or inducing emergence of flat structures with large G4s [387]. The relative amount of mono and bivalent hydrophobic surface area (such as A·G·A·G·A·G·A·G metal ions that stabilize competing structures to various octads) for more efficient binding [379]. As established degree affect the “quadruplex–hairpin” dynamic equilib with the spectral methods and electrophoretic data, the rium characterized by NMR spectroscopy. It was shown r(GGGUUGCGGAGGGUGGGC) sequence from the that the shift of “hairpin duplex–RNA quadruplex” due 5′end region (hTERC) of the human telomerase RNA to potassium ion content regulated maturation of human folded into G4 dimer in K+ solution [392]. It was specifi premicroRNA [82]. Smallmolecule ligands that can cally mentioned that the thermodynamically stable unfold or stabilize RNA quadruplexes can also shift the intramolecular parallel RNA quadruplex contained a sin “quadruplex–hairpin” equilibrium [387, 388]. Interesting gle nucleotide bulge (the cytidine residue underlined in ly, some ligands affect differently the RNA G4s and the the presented sequence) in one of the G4 “edges”. Direct DNA G4s. For example, the cationic porphyrin TmPyP4 experimental evidence for formation of RNA G4s in the stabilized the DNA quadruplex formed by the G4motif fullsized hTERC was also reported [206]. in the cMyc promoter, thus inhibiting transcription of Biological functions of RNA quadruplexes. The stud this oncogene. The same ligand exerts the opposite action ies of recent years have shown that RNA G4s play an on RNA G4s [236] unwinding, for example, the extreme important role in cellular processes [275, 393]. They par ly stable quadruplex formed by the mRNA that encodes ticipate in transcription termination and in regulation of MT3MMP protein, which results in the mitigation of different stages of RNA metabolism, for example, post

BIOCHEMISTRY (Moscow) Vol. 81 No. 13 2016 GQUADRUPLEXES OF NUCLEIC ACIDS 1629 transcriptional gene expression, which included control when the RNA G4 is located in the IRESelement, it over mRNA half lifetime, splicing, and polyadenylation facilitates a new mechanism of capindependent transla of premRNA [15, 394], as well as translation [372, 393, tion initiation [403]. It was reported [404] that RNA G4 395]. Folding of G4motifs in RNA sequences into formed in the IRES of the mRNA encoding human quadruplex structure affecting translation can be espe VEGF protein directly involved in interaction with the cially important in plants and other organisms, where cel 40S ribosome subunit. In the review published in 2015, lular ionic conditions, e.g. the concentration of potassi the role of RNA G4s in regulation of processing and um ions, can be changed as a result of stress [373]. functioning of noncoding RNAs was discussed [20]. Until recently, the G4s formed in different mRNA These are promising new objects for investigation of G4 regions were considered as a network of translation functions in the context of various neurodegenerative dis repressors. It was shown that RNA Gquadruplexes local eases. ized in 5′UTR mRNA encoding the NRAS, Bcl2, Zic Several publications in recent years have been devot 1, TRF2, MT3, and ESR proteins inhibited translation, ed to investigation of biological functions of the TERRA although the exact mechanism of the inhibition by RNA telomeric repeats and quadruplex structures formed by G4s was not understood. It has been mentioned that the these noncoding RNAs. It was shown that TERRA was level of translation repression could reach 50% (for most not only accumulated in the cell nucleus, but it was colo G4motifs) and even 80%. The RNA quadruplexes calized with telomeric DNA at the chromosome ends formed in the 3′UTR mRNA [375] and in the mRNA (FISH, Fluorescence In situ Hybridization method) and open reading frame also inhibit translation elongation in with proteins of telomere shelterin complex (immunoflu vitro and decrease protein synthesis in cells [376]. It was orescence assay) [1]. Participation of TRF2 in simultane shown that G4 localized in the coding regions of mRNA ous binding to TERRA in the form of a G4 and to telom can stimulate reading frame shift in vitro and in cell cul eric DNA as a duplex or G4 (ELISA, Enzyme Linked ture, with this effect correlating with quadruplex stability, ImmunoSorbent Assay) provides evidence that TERRA is which can be modulated by G4binding small molecules the key component of the telomere machinery [267]. [396]. During the process, one TERRA molecule, which can To inhibit translation of the target mRNA, the fol fold into a quadruplex garland [192], can interact with lowing strategy was developed: formation of a bimolecu several TRF2 molecules [267]. It has been suggested that lar hybrid DNA–RNA G4 was initiated in the predeter TERRA represses its own transcription and participates mined regions of mRNA containing only two Gtracts in maintenance of telomere structure and formation of using modified oligodeoxyribonucleotides with design heterochromatin [405]. It was shown that TERRA caused allowing targeted addition of missing Gtracts required changes in gene expression in human cancer cells in vivo. for G4 formation [397]. It was shown using the mRNA The telomeric RNA that forms G4s inhibits expression of encoding eIF4E protein, which was actively expressed in genes associated with the innate immune system, thus various malignant tumors, that formation of Gquadru affecting tumor malignancy [406]. plexes in the 5′UTR mRNA and in the protein coding It is interesting that the TERRA repeats, 5′ region of the eIF4E mRNA initiated by phosphoro UUAGGG3′, are complementary to the telomerase thioate derivatives of oligonucleotides resulted in 30 and RNA sequence. It was shown using in vitro reconstructed 60% inhibition of expression of this protein in human telomerase and synthetic TERRA molecule that the cancer cells, respectively [397]. On the contrary, addition TERRA repeats hybridized with the enzyme RNA of antisense oligonucleotides (complementary to the G4 inhibiting its activity. However, the inhibiting action of motif) can result in the destruction of RNA G4 [398]. TERRA upon telomerase can be mitigated in vivo by the The effect of antisense peptide nucleic acids on RNA heterogeneous nuclear ribonucleoprotein A1 (hnRNPA1) quadruplex assembly in vitro with relatively high degree of involved in the control of telomere length [407]. It has discrimination between the different G4motifs has been been suggested that the enzymatic elongation of telomer described [399]. This approach – unwinding of RNA G4 ic ends required a balance between the levels of TERRA by 1719nt oligonucleotides – was successfully used for and hnRNPA1 protein functioning as regulators of enzy twofold change in the level of inhibition of specific matic activity. The role of Gquadruplexes in RNA biol mRNA translation in human cells [400]. ogy, including TERRA telomeric repeats and telomerase However, it was recently shown that modulation of RNA component hTERC, has been discussed in the translation depended on the nucleotide context in which recent reviews [394, 408]. G4motifs were located. The formed RNA quadruplexes From the practical point of view, a study in which can either inhibit or activate gene expression depending G4containing RNA aptamer produced by in vitro selec on their location in the 5′UTR mRNA [393, 401, 402]. tion activated fluorescence of a ligand similar to green It has been suggested that the neighboring base fluorescent protein is of great interest [409]. The sequences, intracellular environment, and interacting approach was developed recently based on the replace partners can affect the functions of G4 in the cell. Indeed, ment of pyrimidine residues in the loops of telomeric G4s

BIOCHEMISTRY (Moscow) Vol. 81 No. 13 2016 1630 DOLINNAYA et al. with fluorescent 5benzofuran derivatives of 2′deoxyuri The probe was designed in a way that it can form a hair dine and uridine, which allowed the development of pin structure in the absence of target and, hence, the switchable fluorescent probes for discrimination of DNA FAM fluorescence was quenched by the DABCYL quadruplexes of different topology and parallel RNA G4 quencher located at the other end of the molecule. [410]. These G4 sensors were also used for estimation of Formation of the hybrid quadruplex with telomeric RNA the specificity and affinity of low molecular weight lig forced the DNAhairpin to open, which resulted in fluo ands to quadruplexes of various chemical nature and con rescence enhancement because the fluorophore and formation. quencher were separated. This effect was observed after penetration of the DNA beacon into HeLa cells, con firming intracellular formation of the telomeric hybrid HYBRID DNA–RNA GQUADRUPLEXES G4 [411]. It was shown in the same work that quadru plexes containing telomeric DNA and RNA could con Hybrid DNA–RNA Gquadruplexes are also func tribute to the protection of telomeric ends. It is known tionally important. The possibility of association between that telomeric singlestranded DNA forms a quadruplex telomeric DNA and TERRA via formation of hybrid garland. Formation of G4 structures of higher order is DNA–RNA quadruplex with parallel topology was inves also characteristic for telomeric RNA [381]. tigated for the first time in [411]. Formation of such Intermolecular interaction of the DNA and RNA end structures in vitro was established by several independent repeats can lead to formation of hybrid G4, which is and complementary methods using oligonucleotide mod located at the interface of the structured telomeric DNA els. To prove occurrence of the hybrid G4s in the cellular sequences and TERRA and can provide protective effect medium, telomeric DNA and RNAoligonucleotides creating steric hindrance [411]. Moreover, it is known labeled with different fluorophores (FAM and Cy3) at the that the telomeric protein of shelterin complex TRF2 3′ends were transfected into HeLa cells. The observed binds simultaneously DNA G4 and RNA G4, thus bring change in the color of signal occurring during colocaliza ing them closer together in the cell [267]. tion of fluorophores served as evidence that they were The hybrid DNA–RNA G4s can be a predominant brought together in the hybrid bimolecular G4. If the form of quadruplexes also in the transcription process. DNA and RNAprobes were not interacting, there They are formed from the nontemplate DNA sequence would be two different fluorescence signals. The addition and the RNA transcript [412]. It was shown that the al brilliant evidence of the hybrid telomeric G4 formation DNA–RNA G4s modulated transcription under in vitro in live cells was based on the use of a chemical approach and in vivo conditions, and it was precisely these struc [411]. The DNA probe (12mer with two telomeric tures that comprised the major form of G4 that were repeats) contained an azidocoumarin residue at the 5′ involved in the transcription process. The fact that the end, and the 12nt RNA – a 5′alkyne group. Azido RNA transcript is involved in the formation of hybrid G4 coumarin was selected as a profluorophore with was confirmed by demonstrating that the effect of tran quenched fluorescence by the electronrich αnitrogen of scription inhibition was achieved on addition of GTP the azido group. However, the synthesis of the triazole participating in the RNA synthesis, and its replacement ring by alkyneazide cycloaddition is accompanied by the by the 7deazaGTP, which was not capable of Gtetrad emergence of a strong fluorescence signal due to disap formation restored the transcription level. These results pearance of the quenching effect (Fig. 9). Hence, the flu indicate that the intermolecular DNA–RNA G4s are orescence enhancement could indicate formation of the more involved in the regulation of transcription and relat hybrid parallel G4 in which the cycloaddition reaction ed processes than the intramolecular DNA quadruplexes was initiated due to bringing the reactive groups at the formed by the template strand of the double helix [412]. ends of RNA and DNAoligonucleotides into proximity. The fact that only two Gtracts on the nontemplate Bright blue fluorescence was observed (using a fluores DNA strand participate in formation of hybrid G4 seems cence microscope) following addition of the cellular especially important, because as was shown with bioinfor medium containing copper catalyst to the HeLa cells matics techniques these motifs are more abundant in the incubated with the oligonucleotides. It was established transcribed regions of the genome than the intramolecu that the simple molecular colocalization of oligomers did lar DNA quadruplex formation motifs containing four not initiate the reaction of cycloaddition. The fact that and more Gtracts on the template strand [413]. The this method was successfully used to demonstrate the for hybrid quadruplex motifs, which are evolutionarily con mation of hybrid RNA–DNA G4 in solution in vitro served [413], are abundant in the genomes of warm agrees with the experimental data with the cells [411]. blooded animals [414] and occur in more than 97% of The formation of hybrid G4 between the natural telomer human genes [412]. The folding mechanism of hybrid ic RNA (TERRA) and oligodeoxyribonucleotide con G4s associated with transcription allows controlling their taining telomeric repeats with fluorescence label at both formation and, consequently, the transcription level. For ends was observed under conditions close to native ones. example, the presence of Crich oligonucleotides com

BIOCHEMISTRY (Moscow) Vol. 81 No. 13 2016 GQUADRUPLEXES OF NUCLEIC ACIDS 1631 plementary to the RNA transcript prevents formation of stress of the DNA [419]. It should be also taken into the hybrid G4, and the quadruplexspecific ligands stabi account that in vitro experiments are commonly conduct lize these structures [414]. ed in dilute solutions, i.e. under conditions that are sig According to some published data [415], quadruplex nificantly different from the molecular crowding charac hybrids can be involved also in regulation of DNA syn teristic of in vivo systems. Moreover, smallmolecule lig thesis, at least in mitochondria, where the transcription ands can shift the equilibrium towards quadruplex struc machine generates RNA primers required for initiation of ture formation by stabilizing their structure, which can replication. The DNA of the nontemplate strand con skew the real distribution pattern of these noncanonical taining fragments with Grich conserved sequence 5′ structures in the cell DNA. Nevertheless, direct evidence GGGGGAGGGGGGG (two Gtracts) from human of the G4 existence in the gene promoter region was mitochondrial DNA and the formed transcript fold into a reported as early as 2002. However, this and similar stud stable hybrid G4 with parallel topology close to the origin ies were based on the biological effects of G4stabilizing of replication. The 3′end of the primer in this quadru ligands introduced into the cell. The discovery of G plex is removed from the template strand and is not acces quadruplex structures at the telomeres in macronuclei of sible to the action of the mitochondrial replication the Stylonychia lemnae ciliate using fluorescent antibodies machinery, which explains the mechanism of negative was an important breakthrough in this research area. It regulation of the DNA replication. Only after unwinding was shown later that the G4 formation depended on the of the G4 with helicase (such as, for example, evolution phase of the cell cycle and was controlled by proteins arily conserved Pif1) the released primer can be used for binding to the telomeric ends. Only in studies of recent initiation of the DNA replication. Participation of hybrid years the possibility to visualize the loci in mammalian quadruplexes in immunoglobulin gene recombination cells (including human cells), which adopt the G4 struc and in neurodegenerative diseases caused by expansion of tures, and to elucidate their role in the cascade of biolog Grich repeats in the C9orf72 [416] and FMR1 [417] ical events has been achieved. genes has also been discussed. Two independent lines of evidence demonstrated the genomewide distribution of G4 structures in human cancer cells [203]. In the first approach, a highly selected EVIDENCE FOR DNA AND RNA QUADRUPLEX G4binding smallmolecule ligand, pyridostatin, was OCCURRENCE IN CELL CULTURES AND in vivo used to target polymorphic G4s regardless of their topol ogy. Pyridostatin was shown to promote growth arrest in Over several decades, the possibility of formation of cells and modulate the expression of the genes containing biologically relevant Gquadruplexes in live cells that G4motifs by inducing replication and transcription were unlike the other noncanonical DNA structures sta dependent DNA damage. It was suggested that the ligand ble under physiological condition has been discussed prevented the polymerase movement along the double among scientists. The discovery of ligands specific to G4 helix by stabilizing the G4s, which resulted in a DNA structures provided a tool for investigation of the proper break caused by the physical forces acting on a substrate ties of such structures, as well as for development of or by endonuclease activity. A chromatin immunoprecip methods for their isolation and identification in cells itation sequencing analysis of the DNA damage marker [205]. The chromatin immunoprecipitation analysis was provided the genome distribution of pyridostatininduced used to determine the localization of G4s in the genome. damaged loci. A chemical approach (reaction of alkyne The chromatin fragments were fractionated depending on azide cycloaddition of fluorescent group to pyridostatin) their affinity to quadruplexbinding ligands followed by was used in the independent series of experiments to visu analysis of selected samples using sequencing or template alize the ligand molecules in the cell nuclei as fluorescent analysis on microchips. Identification of G4s in cellular signals. The regioselective reaction of the alkyne group cultures was also performed using monoclonal antibodies attached to pyridostatin with the azide group on the fluo highly specific to these structures [320]. rescent dye Alexa Fluor was initiated in cellulo by a cop The complexity of G4 testing in live cells and ambi per catalyst. Loci with folded Gquadruplex structures in guity of interpretation of the results is related to many human cell DNA were revealed by highresolution factors. Numerous proteins and enzymes existing in vivo microscopy, and it was shown that they were located pre can interact with noncanonical DNAs, thus stabilizing dominately in the regions away from the chromosome or destabilizing these structures [418], as well as cleaving ends. The hPif1 helicase, known for its high selectivity them. The genome regions containing G4motifs can be towards G4 and regulation of these structures formation included in nucleosomes, where they are completely and processing in the genome, was used as a second refer shielded by histone proteins. Rearrangement of the ence point. Distribution of helicase signals in the cell genome G4motif region into the Gquadruplex structure nuclei in comparison with the fluorescently labeled pyri depends on the factors affecting stability of the double dostatin was investigated on the human osteosarcoma cell helix: the degree of methylation and local topological lines expressing human helicase fused to green fluores

BIOCHEMISTRY (Moscow) Vol. 81 No. 13 2016 1632 DOLINNAYA et al. cent protein. This analysis showed that the helicase was plexes, and this opened new possibilities for targeted reg bound to G4motifs in the genome even without the lig ulation of cellular processes such as inhibition of onco and treatment. The general distribution pattern of fluo gene expression. rescent signals was comparable with that observed for the These data were corroborated by the work of anoth labeled small molecules. In an independent experiment er scientific group [421] where highly specific G4anti with cells fixed by formaldehyde “freezing” all biological bodies were also used. The increase in the number of processes prior to the pyridostatin treatment significant detected G4s in nuclei of human cells was observed under overlapping between the genomic targets of pyridostatin the action of two G4stabilizing ligands – telomestatin and helicase was observed. These data indicate the exis and TMPyP4. Intracellular optical visualization of DNA tence of the preformed G4 in human cells, formation of G4s using fluorogenic ligands was described [259]. Very which was not initiated by addition of the G4binding lig recently, a report was published [422] where direct evi and. dence of the existence of DNA quadruplexes in cell mito Not all the sites with high content of G4motifs were chondria was presented. Fluorescent G4specific ligands labeled with the fluorescent ligand. It is likely that addi based on carbazole derivatives that can migrate from the tional mechanisms facilitating G4 folding should be real nucleus to mitochondria of malignant cells were used for ized. Negative supercoiling of DNA in a certain locus or visualization of quadruplexes by confocal microscopy. It activity of replication or transcription processes that are should be noted that in the case of normal cells they accu accompanied by local melting of the double helix and mulated in the cytoplasm. The developed compounds shortlived release of singlestranded regions for reading were shown to stabilize G4s and, hence, to inhibit expres by polymerase could serve as examples of such mecha sion of mitochondrial genes acting as antitumor agents. nisms. The ability of G4motif to form quadruplex and In addition to DNA G4s, the ribonucleotide analogs bind the ligand could also depend on whether the Grich of quadruplexes and their role in RNA biology have regions are on the transcribed or nontranscribed strand aroused considerable and growing interest [394]. Direct of the gene [368] or, in the case of replication, on the evidence of formation of RNA quadruplexes in human leading or lagging DNA strand. It also must be taken in cells was presented in [319], in which the detection of G consideration that certain cellular effects of G4specific quadruplexes was conducted in the cell cytoplasm by G4 ligands might be caused by their interaction with RNA specific BG4 antibody. Prior to that it was shown by G4s [420]. ELISA that this antibody recognized the major structural Direct quantitative visualization of DNA G4 struc determinant of G4s effectively binding to both DNA and tures in human tumor cells using quadruplexspecific RNA quadruplexes. The endogenous G4s were visualized antibody has been described [318]. The visualization was by fluorescence microscopy in normal, immortalized, achieved via amplification of the fluorescent signal in an and malignant human cells. The fluorescence signals were antibody sandwich. The loss of signals on preincubation amplified using a sandwich of labeled antibodies; BG4 of the antibody with excess of preformed G4 oligonu served as a primary antibody in the process. Both the cleotides as well as during incubation of the cells with intranuclear signals assigned to the DNA quadruplexes fluorescent antibodies in the absence of the primary G4 and the fluorescence signals (with longer exposure) dis binding antibody indicated specificity of the signal. The tributed in the cytoplasm of all the investigated cell lines colored loci in the nucleus also disappeared during treat and corresponded to RNA G4s were identified using the ment of the cells with DNase, but not with RNase. described approach. Cell staining with the CellMask Location of the signals at the ends of metaphase chro green fluorescent dye, which revealed cell boundaries, mosomes confirms the presence of G4s at the telomeric corroborated cytoplasmic location of the primary BG4 ends, and the scattering of the signals in other chromo antibody. When fixed permeabilized cells were treated some loci indicates that most Gquadruplex structures with RNase A prior to addition of the BG4 antibody, the (approximately 75%) can be formed in promoter regions quadruplex signals in the cytoplasm disappeared, which and in other DNA regions despite the presence of com indicated the presence of RNA G4s. Along with the peting complementary strand (Fig. 10). It was shown in immunofluorescence assay, low molecular weight ligands this excellent work that formation of G4s in cell nuclei were used to provide evidence of the occurrence of was modulated depending on the phase of the cell cycle; endogenous RNA quadruplexes in human cells. For maximum level was observed in the phase of active DNA example, carboxypyridostatin, which was shown by replication (Sphase), which was 4.8fold higher than chemical approaches (alkyneazide cycloaddition in situ) the level of G4 detection in the resting phase. According to bind more effectively to RNA G4 than to the DNA to these data, addition of smallmolecule ligands stabi analogs [235], increased (approximately 2.4fold) the lizing endogenous DNA quadruplexes resulted in an number of G4s only in the cell cytoplasm, not affecting increase (2.9fold) of the amount of detected G4 targets the number of DNA quadruplexes with nuclear localiza in the cell nucleus, which indicated the shift of the tion. Recently, RNA G4 were found in live cells using a duplex–G4 equilibrium towards formation of quadru new generation of quadruplexspecific compound, N

BIOCHEMISTRY (Moscow) Vol. 81 No. 13 2016 GQUADRUPLEXES OF NUCLEIC ACIDS 1633 TASQ, which combined functions of the “smart” ligand and “smart” fluorescence probe [263]. These compounds behave as intracellular molecular sensors targeting only the preformed G4s. They use G4quadruplexes as a tem plate for selfassembly of the artificial Gtetrad, forma tion of which causes fluorescence enhancement. N TASQ exhibits unique properties because, unlike the quadruplexspecific antibodies, it does not require fixa tion and permeabilization of the cells. It was shown that Fig. 9. Evidence of formation of DNA–RNA hybrid telomeric under the conditions used the cytoplasmic RNA G4s (in G4 in HeLa cells using the alkyneazide cycloaddition reaction. free state and more likely in the form of complex ribonu The 12nt DNA with two telomeric repeats (G residues highlight cleoprotein subcellular ensembles) served as targets of the ed with green color) contained an azidocoumarin residue at the 5′end, where fluorescence was quenched by the electronrich α NTASQ, and they were revealed as intensive discrete loci nitrogen in the azide group, and the 12nt RNA (G residues in human breast cancer and osteosarcoma cells as well as marked with red) containing the 5′alkyne group. Synthesis of a in murine melanoma. Moreover, the cells were not pre triazole ring on addition of copper catalyst was accompanied by treated in the process. It has been suggested that NTASQ the emergence of strong fluorescence signal due to disappearance of the quenching effect. penetrates easily through the cytoplasmic membrane, accumulating in the cytoplasm under nondenaturing physiological conditions. ed number of G4positive nuclei in tissues of liver and It was shown [423] that G4specific BG4 antibody stomach cancer patients in comparison with healthy tis could be used to stain DNA G4 structures in human tis sues was observed. To identify malignant tissue transfor sues using immunohistochemistry. A significantly elevat mation, the G4binding fluorescent ligand 3,6bis(1

a b

c d e

Fig. 10. Visualization of endogenous DNA G4 structures in metaphase chromosomes isolated from HeLa cancer cells by immunofluores cence microscopy (using G4specific antibody BG4). The fluorescent foci are concentrated both within the nontelomeric region (ac) and at telomeres (d and e). The symmetric appearance of the foci in the sister chromatids (e) indicates formation of Gquadruplexes in the same locations on the newly replicated DNA. This figure is partly adapted from Fig. 3 in [318].

BIOCHEMISTRY (Moscow) Vol. 81 No. 13 2016 1634 DOLINNAYA et al. methyl4vinylpyridinium) carbazole diiodate was also 2. Huppert, J. L., Bugaut, A., Kumari, S., and Balasubramanian, used [424]. It was found that the number of signals S. (2008) Gquadruplexes: the beginning and end of UTRs, increased depending on the degree of cell transformation, Nucleic Acids Res., 36, 62606268. making this approach promising for early diagnostics of 3. Bochman, M. L., Paeschke, K., and Zakian, V. A. (2012) oncological diseases. DNA secondary structures: stability and function of G The Gquadruplex structures were identified by quadruplex structures, Nat. Rev. Genet., 13, 770780. 4. Lipps, H. J., and Rhodes, D. (2009) Gquadruplex struc immunoelectron microscopy in samples from different tures: in vivo evidence and function, Trends Cell Biol., 19, organisms: ciliates, flatworms, fruit flies, and mammals 414422. [425]. It was found that the loci stained by the 1H6 5. Valton, A. L., HassanZadeh, V., Lema, I., Boggetto, N., monoclonal antibodies, which were specific to DNA G4s Alberti, P., Saintome, C., Riou, J. F., and Prioleau, M. of various topologies, were present in heterochromatin of N. (2014) G4 motifs affect origin positioning and efficien all samples. It was found that the sites of 1H6 antibody cy in two vertebrate replicators, EMBO J., 33, 732 binding in the polytene chromosomes from drosophila 746. salivary glands were colocalized with heterochromatic 6. Foulk, M. S., Urban, J. M., Casella, C., and Gerbi, S. A. proteins. It was also observed that the somatic cells in dif (2015) Characterizing and controlling intrinsic biases of ferent organisms displayed more intensive staining than lambda exonuclease in nascent strand sequencing reveals pluripotent stem cells. These findings indicate a con phasing between nucleosomes and Gquadruplex motifs served role of G4s in nuclear organization and cell differ around a subset of human replication origins, Genome Res., entiation. It is the authors’ opinion that the Gquadru 25, 725735. plex structures are present in postmitotic cells as well as in 7. Paeschke, K., Juranek, S., Simonsson, T., Hempel, A., Rhodes, D., and Lipps, H. J. (2008) Telomerase recruit mitotic chromosomes. They can exist independently of ment by the telomere end binding proteinbeta facilitates DNA replication, transcription, or recombination stimu Gquadruplex DNA unfolding in ciliates, Nat. Struct. Mol. lating genetic instability. Biol., 15, 598604. 8. Balasubramanian, S., Hurley, L. H., and Neidle, S. (2011) The studies conducted in recent years have shown Targeting Gquadruplexes in gene promoters: a novel anti that G4s exist in genomic DNA in all phases of the cell cancer strategy? Nat. Rev. Drug Discov., 10, 261275. cycle. These noncanonical structures are diverse. On one 9. Kruisselbrink, E., Guryev, V., Brouwer, K., Pontier, D. B., hand, they can perform regulatory functions in the cell, Cuppen, E., and Tijsterman, M. (2008) Mutagenic capa inhibit oncogene expression, block undesired elongation city of endogenous G4 DNA underlies genome instabi of telomeric DNA, control the level of negative supercoil lity in FANCJdefective C. elegans, Curr. Biol., 18, 900 ing in the genome, and serve as targets of antitumor ther 905. apeutics. Recently, the role of Gquadruplexes in embryo 10. Beaume, N., Pathak, R., Yadav, V. K., Kota, S., Misra, H. development, which is the most controlled process in ver S., Gautam, H. K., and Chowdhury, S. (2013) Genome tebrate biology, was established [426]. On the other hand, wide study predicts promoterG4 DNA motifs regulate selective functions in bacteria: radioresistance of G4 formation causes genome instability (genomic inver D. radio durans involves G4 DNAmediated regulation, Nucleic sions, recombination, mutations, deletions, and others) Acids Res., 41, 7689. associated with oncological diseases and neurological dis 11. Cahoon, L. A., and Seifert, H. S. (2009) An alternative orders. In this review, we have presented stateoftheart DNA structure is necessary for pilin antigenic variation in knowledge on these amazing structures in all investigated Neisseria gonorrhoeae, Science, 325, 764767. aspects. The most important information on the structure 12. Tarsounas, M., and Tijsterman, M. (2013) Genomes and and biological functions of Gquadruplexes was obtained Gquadruplexes: for better or for worse, J. Mol. Biol., 425, using novel research techniques, and their major features 47824789. were emphasized in this review. 13. 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