THE WINTER 2020 Re p ort CMTA www.cmtausa.org BE THE CHANGE >>>Gene Editing Surgical Correction Youth of Tomorrow 6Studies for Type 2 14of the CMT Foot 18 Shine at NYC Gala CMTA LEADERSHIP Amy J. Gray, CEO BOARD OF DIRECTORS ADVISORY BOARD CMTA STAR ALLIANCE Gilles Bouchard, Chairman Jonah Berger David Misener, BSc (HK), PARTNERS: Gary Gasper, Treasurer Gregory Carter, MD, MS CPO, MBA Herb Beron, Secretary Ken Cornell, CO Elizabeth Misener, PhD, David Coldiron Bob DeRosa LMSW ACCELERON PHARMA Thomas W. Dubensky, Jr., PhD Katy Eichinger, PT, DPT, NCS James Nussbaum, PT, PhD, Laura Fava Ashraf Elsayegh, MD, FCCP SCS, EMT ARQ GENETICS Alan Korowitz Tim Estilow, OTR/L Sabrina Paganoni, MD, PhD David Norcom Shawna Feely, MS, CGC Glenn Pfeffer, MD CHARLES RIVER Steve O’Donnell Valery Hanks, OTR/L, C/NDT Clark Semmes Chris Ouellette Sarah Kesty Carly Siskind, MS, CGC GENZYME, A SANOFI COMPANY Elizabeth Ouellette Kate Lair Greg Stilwell, DPM Kevin Sami Sean McKale, CO, LO David Tannenbaum, LCSW HUMANFIRST THERAPEUTICS LLC Phyllis Sanders, Esq. Bethany Noelle Meloche Amy Warfield, PT, DPT Steven Scherer, MD, PhD Tom Meloche HORIZON DISCOVERY Michael Shy, MD John Svaren, PhD IONIS PHARMACEUTICALS Special Advisor to the Board INFLECTIS BIOSCIENCE Bruce Chizen THE JACKSON LABORATORY STAR ADVISORY BOARD John Svaren, PhD, Chair, Scientific Expert Board NCATS (NIH) Mark Scheideler, PhD, Chair, Therapy Expert Board Michael E. Shy, MD, Co-Chair, Clinical Expert Board NEW YORK STEM CELL FOUNDATION Mary Reilly, MD, Co-Chair, Clinical Expert Board PASSAGE BIO CMTA STAFF PSYCHOGENICS Andi Cosby National Events Manager,
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